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Company ReportsOrphan Medical
Orphan Medical
An orphan drug is a pharmaceutical agent developed to treat medical conditions which, because they are so rare, would not be profitable to produce without government assistance. The conditions are referred to as orphan diseases.
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Marketed Drugs
Clinical Trials
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Marketed Drugs
Therapeutic Areas:
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Classification:
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Include Generics:
Trade Name
Drug Name
Approved
Patent Expires
Indication
AlprolixEftrenonacog alfa2016-05-12
AspaveliPegcetacoplan2021-12-132026-2038
DopteletAvatrombopag2019-06-202027
EloctaEfmoroctocog alfa2015-11-18
GamifantEmapalumab2018-11-20
KepivancePalifermin2004-12-15
KineretAnakinra2001-11-14
OrfadinNitisinone2002-01-182033-2035
SynagisPalivizumab1998-06-19
XiapexCollagenase clostridium histolyticum2011-02-28
ZynlontaLoncastuximab tesirine2022-12-20
Clinical Trials
Therapeutic Areas:
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Classification:
All
Approval:
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Status:
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Phases:
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Drug Name
Phase 1
Phase 2
Phase 3
Phase 4
Indication
Anakinra
1
2
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