PTC Therapeutics - PharmaKB

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Company ReportsPTC Therapeutics

PTC Therapeutics(PTCT)

PTC Therapeutics is a US pharmaceutical company focused on the development of orally administered small molecule drugs and gene therapy which regulate gene expression by targeting post-transcriptional control (PTC) mechanisms in orphan diseases.

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Financial

Marketed Drugs

Clinical Trials

Financial

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*Currency in USD

Company Revenue

Quarterly

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Annual

Annual

Projections

*Quarterly sales USD (in millions)

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Revenue by Drug

Marketed Drugs

Therapeutic Areas:

All

Classification:

All

Include Generics:

Trade Name	Drug Name	Approved	Patent Expires	Indication
Emflaza	Deflazacort	2017-02-09		Inflammation , Duchenne muscular dystrophy
Translarna	Ataluren	2014-07-31		Duchenne muscular dystrophy
Upstaza	Eladocagene exuparvovec	2022-07-18		Inborn errors amino acid metabolism

Clinical Trials

Therapeutic Areas:

All

Classification:

All

Approval:

All

Status:

All

Phases:

All

Drug Name

Phase 1

Phase 2

Phase 3

Phase 4

Indication

healthy volunteers/patients

,

renal insufficiency

,

,

hepatic insufficiency

,

muscular dystrophies

,

duchenne muscular dystrophy

,

limb-girdle muscular dystrophies

ELADOCAGENE EXUPARVOVEC

argininosuccinic aciduria

,

phenylketonurias

,

breast neoplasms

,

central nervous system neoplasms

,

nervous system neoplasms

,

,

myeloid leukemia acute

,

myeloid leukemia

,

,

,

neurofibromatosis 2

,

neurofibromatosis 1

,

neurofibromatoses

,

,

,

coronavirus infections

,

,

urologic neoplasms

,

urethral neoplasms

,

transitional cell carcinoma

,

ureteral neoplasms

,

pelvic neoplasms

,

urinary bladder neoplasms

renal cell carcinoma

,

,

uterine cervical neoplasms

,

,

chronic hepatitis d

,

,

rheumatoid arthritis

,

,

,

,

chronic hepatitis c

,

chronic hepatitis

healthy volunteers/patients

,

alzheimer disease

,

female genital neoplasms

,

,

chronic hepatitis b

,

,

major depressive disorder

,

depressive disorder

,

triple negative breast neoplasms

,

pancreatic neoplasms

,

coronary disease

,

coronary artery disease

,

myocardial ischemia

,

,

,

sickle cell anemia

,

,

,

,

precursor cell lymphoblastic leukemia-lymphoma

,

parkinson disease

,

autistic disorder

,

autism spectrum disorder

,

pervasive child development disorders

,

chronic hepatitis

,

rectal neoplasms

,

,

,

,

b-cell chronic lymphocytic leukemia

,

lymphoid leukemia

,

,

nasopharyngeal carcinoma

,

nasopharyngeal neoplasms

,

stomach neoplasms

,

esophageal neoplasms

,

,

neoplasm metastasis

,

antiphospholipid syndrome

,

respiratory insufficiency

,

,

colorectal neoplasms

,

non-small-cell lung carcinoma

,

lupus nephritis

,

human influenza

,

breast neoplasms

,

,

large b-cell lymphoma diffuse

,

b-cell lymphoma

,

non-hodgkin lymphoma

,

myeloid leukemia acute

,

multiple sclerosis

,

,

hepatocellular carcinoma

,

colonic neoplasms

,

thrombocytopenic purpura idiopathic

,

liver cirrhosis

,

neuromyelitis optica

,

membranous glomerulonephritis

,

chronic progressive multiple sclerosis

,

relapsing-remitting multiple sclerosis

,

nephrotic syndrome

,

ovarian neoplasms

,

ovarian epithelial carcinoma

,

,

hemolytic anemia autoimmune

,

,

chronic hepatitis c

,

,

,

rheumatoid arthritis

,

,

,

juvenile arthritis

,

,

follicular lymphoma

,

,

,

myelodysplastic syndromes

,

,

,

acquired immunodeficiency syndrome

,

kidney transplantation

,

drug-related side effects and adverse reactions

,

heart disease risk factors

,

cognitive dysfunction

allergic rhinitis seasonal

,

nasal obstruction

,

,

,

restless legs syndrome

,

spinal cord injuries

,

type 1 diabetes mellitus

,

,

non-small-cell lung carcinoma

,

,

breast neoplasms

,

,

neurologic manifestations

,

wounds and injuries

,

central nervous system diseases

,

spinal cord diseases

,

sleep wake disorders

,

inguinal hernia

,

peripheral nervous system diseases

,

,

,

,

healthy volunteers/patients

,

,

partial epilepsies

,

diabetic neuropathies

,

,

,

sleep initiation and maintenance disorders

,

,

postherpetic neuralgia

,

postoperative pain

,

anxiety disorders

,

,

generalized anxiety disorder

,

complex partial epilepsy

,

,

,

bronchiolitis obliterans syndrome

,

,

,

intractable pain

,

,

,

renal insufficiency

,

pharmacovigilance

ovarian neoplasms

,

ovarian epithelial carcinoma

,

,

diffuse intrinsic pontine glioma

,

,

Bos taurus adrenal cortex corticosteroids

multiple sclerosis

,

neuromyelitis optica

,

,

bacterial infections

,

bacterial skin diseases

,

,

bacterial pneumonia

,

,

soft tissue infections

,

infectious skin diseases

,

community-acquired infections

,

ventilator-associated pneumonia

,

iatrogenic disease

,

healthcare-associated pneumonia

,

urinary tract infections

,

fallopian tube neoplasms

,

ovarian epithelial carcinoma

,

endometrial neoplasms

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