Company Reports
Company Reports
Drug Reports
Drug Reports
Disease Reports
Disease Reports
Sets
Sets
Favorites
Favorites
Log in
Log in
About
Pricing
Company Reports
PTC Therapeutics
PTC Therapeutics
(PTCT)
PTC Therapeutics is a US pharmaceutical company focused on the development of orally administered small molecule drugs and gene therapy which regulate gene expression by targeting post-transcriptional control (PTC) mechanisms in orphan diseases.
Download report
Favorite
Financial
Marketed Drugs
Clinical Trials
Financial
Stock price
*Currency in USD
Company Revenue
Quarterly
Quarterly
Annual
Annual
Projections
*Quarterly sales USD (in millions)
Mock data
Subscribe for the real data
Revenue by Drug
Marketed Drugs
Therapeutic Areas:
All
Classification:
All
Include Generics:
Trade Name
Drug Name
Approved
Patent Expires
Indication
Emflaza
Deflazacort
2017-02-09
Inflammation
,
Duchenne muscular dystrophy
Translarna
Ataluren
2014-07-31
Duchenne muscular dystrophy
Upstaza
Eladocagene exuparvovec
2022-07-18
Inborn errors amino acid metabolism
Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Drug Name
Phase 1
Phase 2
Phase 3
Phase 4
Indication
Ataluren
healthy volunteers/patients
,
aniridia
,
hemophilia a
,
hemophilia b
,
colorectal neoplasms
,
endometrial neoplasms
,
epilepsy
,
myoclonic epilepsies
,
inborn errors metabolism
,
inborn errors amino acid metabolism
,
duchenne muscular dystrophy
,
muscular dystrophies
,
fibrosis
,
cystic fibrosis
,
inborn genetic diseases
,
muscular diseases
,
nervous system diseases
,
musculoskeletal diseases
,
x-linked genetic diseases
,
neuromuscular diseases
,
atrophic muscular disorders
Deflazacort
healthy volunteers/patients
,
renal insufficiency
,
liver diseases
,
hepatic insufficiency
,
muscular dystrophies
,
duchenne muscular dystrophy
,
proteinuria
,
neuromuscular diseases
,
membranous glomerulonephritis
,
aspergillosis
,
allergic bronchopulmonary aspergillosis
,
pulmonary aspergillosis
,
limb-girdle muscular dystrophies
,
inborn genetic diseases
,
muscular diseases
,
nervous system diseases
,
musculoskeletal diseases
,
x-linked genetic diseases
,
atrophic muscular disorders
,
chronic renal insufficiency
,
postoperative pain
,
trismus
,
impacted tooth
,
kidney diseases
,
iga glomerulonephritis
,
immunosuppression therapy
,
asthma
ELADOCAGENE EXUPARVOVEC
argininosuccinic aciduria
Sepiapterin
gastroparesis
,
phenylketonurias
Vatiquinone
tic disorders
,
tourette syndrome
,
tics
,
mitochondrial diseases
,
rett syndrome
,
muscular diseases
,
syndrome
,
inborn errors lipid metabolism
,
noise-induced hearing loss
,
angelman syndrome
,
autistic disorder
,
autism spectrum disorder
,
ataxia
,
friedreich ataxia
,
cerebellar ataxia
,
parkinson disease
,
optic nerve diseases
,
emergencies
,
hereditary optic atrophy leber
Emvododstat
neoplasms
,
breast neoplasms
,
central nervous system neoplasms
,
nervous system neoplasms
,
leukemia
,
myeloid leukemia acute
,
myeloid leukemia
,
sarcoma
,
kaposi sarcoma
,
neurofibromatosis 2
,
neurofibromatosis 1
,
neurofibromatoses
,
neurofibroma
,
covid-19
,
coronavirus infections
,
coronavirus
,
pneumonia
Gilvetmab
head and neck neoplasms
,
castration-resistant prostatic neoplasms
,
urologic neoplasms
,
ovarian neoplasms
,
triple negative breast neoplasms
,
endometrial neoplasms
,
thyroid neoplasms
,
squamous cell carcinoma
,
squamous cell neoplasms
,
local neoplasm recurrence
,
hepatocellular carcinoma
,
liver neoplasms
,
colorectal neoplasms
,
adenocarcinoma
,
stomach neoplasms
,
neoplasm metastasis
,
sarcoma
,
colonic neoplasms
,
rectal neoplasms
,
melanoma
,
cutaneous malignant melanoma
,
pancreatic neoplasms
,
renal cell carcinoma
,
carcinoma
,
non-small-cell lung carcinoma
Alfacalcidol
asthma
,
healthy volunteers/patients
,
non-small-cell lung carcinoma
,
lung injury
,
lung neoplasms
,
smoking
,
family relations
Aspartame
metabolic bone diseases
,
t-cell lymphoma
,
mantle-cell lymphoma
,
large b-cell lymphoma diffuse
,
brain diseases
,
hepatic encephalopathy
,
healthy volunteers/patients
,
recurrence
,
carcinoma
,
anemia
,
precursor cell lymphoblastic leukemia-lymphoma
,
precursor t-cell lymphoblastic leukemia-lymphoma
,
lymphoid leukemia
,
asthma
,
rare diseases
,
cystinosis
,
multiple myeloma
,
plasma cell neoplasms
,
neoplasms
,
leukemia
,
lymphoma
,
coronary disease
,
coronary artery disease
,
myocardial ischemia
,
dyslipidemias
,
psoriasis
,
nasal polyps
,
bone fractures
,
stomatitis
,
mucositis
,
vasculitis
,
anti-neutrophil cytoplasmic antibody-associated vasculitis
,
inborn urea cycle disorders
,
heart failure
,
left ventricular dysfunction
,
cardiovascular diseases
,
hypercholesterolemia
,
hyperlipidemias
,
hidradenitis suppurativa
Bevifimod
drug interactions
,
medical sociology
,
lung neoplasms
,
pharmacokinetics
,
healthy volunteers/patients
,
mesothelioma
,
small cell lung carcinoma
,
pain
,
chronic cough
,
head and neck neoplasms
,
adenocarcinoma of lung
,
gliosarcoma
,
oligodendroglioma
,
neoplasms
,
leukemia
,
b-cell chronic lymphocytic leukemia
,
breast neoplasms
,
hepatocellular carcinoma
,
lymphoid leukemia
,
recurrence
,
t-cell lymphoma peripheral
,
multiple myeloma
,
follicular lymphoma
,
large b-cell lymphoma diffuse
,
glioblastoma
,
astrocytoma
,
ovarian neoplasms
,
colorectal neoplasms
,
myeloproliferative disorders
,
myeloid leukemia
,
preleukemia
,
b-cell lymphoma marginal zone
,
triple negative breast neoplasms
,
liver neoplasms
,
melanoma
,
amyloidosis
,
kidney diseases
,
squamous cell carcinoma of head and neck
,
esophageal squamous cell carcinoma
,
neuralgia
,
diabetic neuropathies
,
peripheral nervous system diseases
,
ovarian epithelial carcinoma
,
endometriosis
,
salivary gland neoplasms
,
x-linked bulbo-spinal atrophy
,
colonic neoplasms
,
spinocerebellar degenerations
,
biphenotypic leukemia acute
,
syndrome
,
t-cell lymphoma
,
graft vs host disease
,
bone marrow transplantation
,
esophageal neoplasms
,
hodgkin disease
,
aplastic anemia
,
waldenstrom macroglobulinemia
,
fallopian tube neoplasms
,
myeloid leukemia chronic-phase
,
b-cell leukemia
,
b-cell lymphoma
,
bronchiolitis obliterans syndrome
,
squamous cell carcinoma
,
squamous cell neoplasms
,
castration-resistant prostatic neoplasms
,
lymphoma
,
non-hodgkin lymphoma
,
macular degeneration
,
renal insufficiency
,
anemia
,
chronic renal insufficiency
,
neoplasm metastasis
,
surgical blood loss
,
blood coagulation disorders
,
myelodysplastic syndromes
,
myeloid leukemia acute
,
non-small-cell lung carcinoma
,
postoperative hemorrhage
,
chronic progressive multiple sclerosis
,
urinary bladder neoplasms
,
adenocarcinoma
,
covid-19
,
respiratory distress syndrome
,
coronavirus infections
,
severe acute respiratory syndrome
,
coronavirus
,
hiv infections
,
acquired immunodeficiency syndrome
,
aids-related complex
,
retinal diseases
,
vision disorders
,
eye diseases
,
blindness
,
hemophilia b
,
intracranial hemorrhages
,
thrombocytopenic purpura idiopathic
,
thrombocytopenia
,
hemophilia a
,
multiple sclerosis
,
relapsing-remitting multiple sclerosis
,
prostatic neoplasms
,
carcinoma
,
hemorrhage
,
renal cell carcinoma
,
hematologic diseases
,
hypertension
,
type 2 diabetes mellitus
,
hemostatic disorders
,
insulin resistance
,
diabetes mellitus
,
carcinoma in situ
,
motor activity
,
macular edema
,
thrombosis
,
atrial fibrillation
,
seroma
,
acute kidney injury
,
cardiomyopathies
Unesbulin
ovarian neoplasms
,
ovarian epithelial carcinoma
,
glioma
,
diffuse intrinsic pontine glioma
,
neoplasms
,
leiomyosarcoma
Bos taurus adrenal cortex corticosteroids
leukemia
,
b-cell chronic lymphocytic leukemia
,
lymphoid leukemia
,
covid-19
,
macular edema
,
uveitis
,
lymphoma
,
atopic dermatitis
,
follicular lymphoma
,
large b-cell lymphoma diffuse
,
b-cell lymphoma
,
non-small-cell lung carcinoma
,
inflammation
,
ischemic optic neuropathy
,
bullous pemphigoid
,
non-hodgkin lymphoma
,
lung neoplasms
,
exanthema
,
lupus nephritis
,
nephritis
,
neuromyelitis optica
,
nasal polyps
,
systemic lupus erythematosus
,
breast neoplasms
,
myasthenia gravis
,
pemphigus
,
multiple sclerosis
,
relapsing-remitting multiple sclerosis
,
chronic progressive multiple sclerosis
,
sclerosis
,
end stage liver disease
,
asthma
,
kidney transplantation
,
rheumatoid arthritis
,
arthritis
,
giant cell arteritis
,
liver transplantation
,
juvenile arthritis
,
heart transplantation
,
kidney diseases
,
arteritis
,
polymyalgia rheumatica
,
hypersensitivity
Lactams
osteomyelitis
,
diarrhea
Mk3475
prostatic neoplasms
,
small cell carcinoma
,
neuroendocrine tumors
,
pancreatic ductal carcinoma
Solumedrol
allergic contact dermatitis
,
contact dermatitis
,
myositis
,
multiple sclerosis
,
relapsing-remitting multiple sclerosis
,
sclerosis
,
large b-cell lymphoma diffuse
,
b-cell lymphoma
,
ovarian neoplasms
,
peripheral nervous system diseases
,
ovarian epithelial carcinoma
,
lymphoma
,
non-hodgkin lymphoma
,
intracranial hemorrhages
,
thrombocytopenic purpura idiopathic
,
thrombocytopenia
,
left ventricular dysfunction
,
ventricular remodeling
,
myocarditis
,
pericarditis
,
microvascular angina
,
vascular remodeling
,
exercise tolerance
,
post-acute covid-19 syndrome
,
prostatic neoplasms
,
eczema
,
patient compliance
,
atopic dermatitis
,
dermatitis
1
2
>
© 2020-2025 Collaborative Drug Discovery Inc. (CDD) |
Terms of Use