

Indication | MeSH | Ontology | ICD-10 | Ph 1 | Ph 2 | Ph 3 | Ph 4 | Other | Total |
|---|---|---|---|---|---|---|---|---|---|
| Mitochondrial diseases | D028361 | EFO_0000591 | — | — | 2 | — | — | — | 2 |
| Rett syndrome | D015518 | Orphanet_778 | F84.2 | — | 2 | — | — | — | 2 |
| Muscular diseases | D009135 | EFO_0002970 | G72.9 | — | 1 | — | — | — | 1 |
| Syndrome | D013577 | — | — | — | 1 | — | — | — | 1 |
| Inborn errors lipid metabolism | D008052 | — | — | — | 1 | — | — | — | 1 |
| Noise-induced hearing loss | D006317 | EFO_1001254 | — | — | 1 | — | — | — | 1 |
| Angelman syndrome | D017204 | Orphanet_72 | Q93.51 | — | 1 | — | — | — | 1 |
| Autistic disorder | D001321 | EFO_0003758 | F84.0 | — | 1 | — | — | — | 1 |
| Autism spectrum disorder | D000067877 | — | F84.0 | — | 1 | — | — | — | 1 |
| Ataxia | D001259 | — | R27.0 | — | 1 | — | — | — | 1 |
Indication | MeSH | Ontology | ICD-10 | Ph 1 | Ph 2 | Ph 3 | Ph 4 | Other | Total |
|---|---|---|---|---|---|---|---|---|---|
| Tic disorders | D013981 | — | F95 | 1 | — | — | — | — | 1 |
| Tourette syndrome | D005879 | EFO_0004895 | F95.2 | 1 | — | — | — | — | 1 |
| Tics | D020323 | — | — | 1 | — | — | — | — | 1 |
Indication | MeSH | Ontology | ICD-10 | Ph 1 | Ph 2 | Ph 3 | Ph 4 | Other | Total |
|---|---|---|---|---|---|---|---|---|---|
| Optic nerve diseases | D009901 | EFO_1001330 | H47.14 | — | — | — | — | 1 | 1 |
| Emergencies | D004630 | — | — | — | — | — | — | 1 | 1 |
| Hereditary optic atrophy leber | D029242 | Orphanet_104 | H47.22 | — | — | — | — | 1 | 1 |
| Drug common name | Vatiquinone |
| INN | vatiquinone |
| Description | Vatiquinone is a small molecule pharmaceutical. It is currently being investigated in clinical studies. |
| Classification | Small molecule |
| Drug class | — |
| Image (chem structure or protein) | ![]() |
| Structure (InChI/SMILES or Protein Sequence) | CC(C)=CCC/C(C)=C/CC/C(C)=C/CC[C@@](C)(O)CCC1=C(C)C(=O)C(C)=C(C)C1=O |
| PDB | — |
| CAS-ID | 1213269-98-7 |
| RxCUI | — |
| ChEMBL ID | CHEMBL1812161 |
| ChEBI ID | — |
| PubChem CID | — |
| DrugBank | — |
| UNII ID | 6O85FK9I0X (ChemIDplus, GSRS) |
