

Indication | MeSH | Ontology | ICD-10 | Ph 1 | Ph 2 | Ph 3 | Ph 4 | Other | Total |
|---|---|---|---|---|---|---|---|---|---|
| Thalassemia | D013789 | EFO_1001996 | D56 | 1 | 1 | — | — | — | 2 |
| Beta-thalassemia | D017086 | Orphanet_848 | D56.1 | — | 1 | — | — | — | 1 |
| Polycythemia vera | D011087 | — | D45 | — | 1 | — | — | — | 1 |
| Polycythemia | D011086 | EFO_0005804 | D75.1 | — | 1 | — | — | — | 1 |
| Drug common name | SAPABLURSEN |
| INN | sapablursen |
| Description | Sapablursen is an oligonucleotide pharmaceutical. It is currently being investigated in clinical studies. |
| Classification | Oligonucleotide |
| Drug class | antisense oligonucleotides |
| Image (chem structure or protein) | ![]() |
| Structure (InChI/SMILES or Protein Sequence) | — |
| PDB | — |
| CAS-ID | — |
| RxCUI | — |
| ChEMBL ID | CHEMBL4650478 |
| ChEBI ID | — |
| PubChem CID | — |
| DrugBank | — |
| UNII ID | DXS4HJC32N (ChemIDplus, GSRS) |
