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Drug ReportsRp103
Rp103
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Commercial
Clinical
Drug
Target
Variants
Financial
Trends
Safety
Events Timeline
5D
1M
3M
6M
YTD
1Y
2Y
5Y
Max
Events
FDA approval date
EMA approval date
Patent expiration date
Study first post date
Last update post date
Start date
Primary completion date
Completion date
Results first post date
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Commercial
No data
Clinical
Clinical Trials
39 clinical trials
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Indications Phases 4
Indication
MeSH
Ontology
ICD-10
Ph 1
Ph 2
Ph 3
Ph 4
Other
Total
Brain diseasesD001927G93.4011
Neuronal ceroid-lipofuscinosesD009472E75.411
Indications Phases 2
Indication
MeSH
Ontology
ICD-10
Ph 1
Ph 2
Ph 3
Ph 4
Other
Total
Leigh diseaseD007888Orphanet_506G31.8233
Mitochondrial diseasesD028361EFO_000059122
Myoclonic epilepsiesD004831EFO_1001900G40.422
Hereditary optic atrophy leberD029242Orphanet_104H47.2222
Chronic progressive external ophthalmoplegiaD017246H49.422
Mitochondrial encephalomyopathiesD01723722
Fanconi syndromeD0051981112
Cystic fibrosisD003550EFO_0000390E84122
Lysosomal storage diseasesD0164641112
Lactic acidosisD000140EFO_1000036E87.2011
Show 11 more
Indications Phases 1
Indication
MeSH
Ontology
ICD-10
Ph 1
Ph 2
Ph 3
Ph 4
Other
Total
AsthmaD001249EFO_0000270J4511
Indications Without Phase
Indication
MeSH
Ontology
ICD-10
Ph 1
Ph 2
Ph 3
Ph 4
Other
Total
Patient complianceD01034911
Inborn errors metabolismD00866111
SchizophreniaD012559EFO_0000692F2011
DepressionD003863F33.911
Major depressive disorderD003865EFO_0003761F2211
Urogenital diseasesD00009164211
HyperpigmentationD01749511
Margins of excisionD00007266211
Epidemiology
Epidemiological information for investigational and approved indications
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Drug
General
Drug common name
INN
Description
Classification
Unknown
Drug class
Image (chem structure or protein)Loading
Structure (InChI/SMILES or Protein Sequence)
Identifiers
PDB
CAS-ID
RxCUI
ChEMBL ID
ChEBI ID
PubChem CID
DrugBank
UNII ID
Target
No data
Variants
No data
Financial
No data
Trends
No data
Safety
Black-box Warning
No Black-box warning
Adverse Events
Top Adverse Reactions
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5 adverse events reported
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