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X4 Pharmaceuticals
X4 Pharmaceuticals
(XFOR)
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Drug Name
Phase 1
Phase 2
Phase 3
Phase 4
Indication
Mavorixafor
healthy volunteers/patients
,
waldenstrom macroglobulinemia
,
melanoma
,
liver failure
,
hepatic insufficiency
,
renal cell carcinoma
,
carcinoma
,
syndrome
,
neutropenia
,
autoimmune diseases
,
shwachman-diamond syndrome
,
barth syndrome
Doconexent
waldenstrom macroglobulinemia
,
leukemia
,
precursor cell lymphoblastic leukemia-lymphoma
,
philadelphia chromosome
,
lymphoid leukemia
,
head and neck neoplasms
,
myeloid leukemia acute
,
gata2 deficiency
,
non-small-cell lung carcinoma
,
glioblastoma
,
esophageal neoplasms
,
carcinoma
,
squamous cell carcinoma
,
squamous cell neoplasms
,
plasma cell neoplasms
,
lung neoplasms
,
non-hodgkin lymphoma
,
immunoglobulin light-chain amyloidosis
,
amyloidosis
,
adenocarcinoma of lung
,
bronchiolo-alveolar adenocarcinoma
,
prostatic neoplasms
,
neoplasms
,
neoplasm metastasis
,
recurrence
,
multiple myeloma
,
hodgkin disease
,
residual neoplasm
,
lymphoma
Aspartame
tuberculosis
,
neoplasms
,
myeloid leukemia acute
,
deficiency diseases
,
paraproteinemias
,
hiv infections
,
precursor cell lymphoblastic leukemia-lymphoma
,
breast neoplasms
,
immune system diseases
,
hematologic neoplasms
,
type 2 diabetes mellitus
,
uveitis
,
metabolic diseases
,
disease
,
glycogen storage disease
,
lipidoses
,
immunoglobulin g4-related disease
,
leukemia
,
myeloid leukemia
,
malaria
,
falciparum malaria
,
whooping cough
,
tetanus
,
diphtheria
,
tetany
,
polycystic kidney diseases
,
autosomal dominant polycystic kidney
,
arthrogryposis
,
recurrence
,
renal insufficiency
,
hematologic diseases
,
blood protein disorders
,
neoplasms by histologic type
,
prostatic neoplasms
,
circulating neoplastic cells
,
x-linked bulbo-spinal atrophy
,
heart transplantation
,
non-small-cell lung carcinoma
,
nasopharyngeal carcinoma
,
nasopharyngeal neoplasms
,
esophageal neoplasms
,
adenocarcinoma
,
neoplasm metastasis
,
aplastic anemia
,
multiple myeloma
,
hypercholesterolemia
,
meningococcal infections
,
plasma cell neoplasms
,
hemolytic anemia autoimmune
,
meningitis
,
meningococcal meningitis
,
stomach neoplasms
,
hemophilia a
,
kidney diseases
,
gaucher disease
,
hemophilia b
,
chronic renal insufficiency
,
hyperphosphatemia
,
multiple sclerosis
,
sclerosis
,
homozygous familial hypercholesterolemia
,
hyperlipoproteinemia type ii
,
pharyngitis
,
tonsillitis
,
healthy volunteers/patients
,
asthma
,
glycogen storage disease type ii
,
atopic dermatitis
,
diabetes mellitus
,
insulin resistance
,
hyperglycemia
,
glycogen storage disease type iii
,
heartburn
,
non-hodgkin lymphoma
,
osteoporosis
,
postmenopausal osteoporosis
,
lymphoma
,
lymphoproliferative disorders
Bevifimod
amenorrhea
,
fertility
,
hepatorenal syndrome
,
nocturia
,
anovulation
,
laron syndrome
,
pituitary dwarfism
,
female infertility
,
hypogonadism
,
diabetes mellitus
,
neurogenic diabetes insipidus
,
postpartum hemorrhage
,
carcinoma
,
infertility
,
prostatic neoplasms
,
nocturnal enuresis
,
syndrome
,
cardiovascular diseases
,
polycystic ovary syndrome
,
cesarean section
,
obstetric delivery
,
aortic valve stenosis
,
eye diseases
,
growth disorders
Globulin, immune
lymphoid leukemia
,
neurologic manifestations
,
gastrointestinal neoplasms
,
thoracic neoplasms
,
herpes zoster
,
small cell carcinoma
,
anus neoplasms
,
digestive system neoplasms
,
lung diseases
,
respiratory tract neoplasms
,
bronchogenic carcinoma
,
endocrine gland neoplasms
,
breast diseases
,
bronchial neoplasms
,
breast neoplasms
,
neoplasm metastasis
,
lymphoma
,
pancreatic neoplasms
,
glioblastoma
,
recurrence
,
brain neoplasms
,
esophageal neoplasms
,
liver neoplasms
,
glioma
,
follicular lymphoma
,
squamous cell neoplasms
,
sarcoma
,
hepatocellular carcinoma
,
non-hodgkin lymphoma
,
b-cell lymphoma
,
cholangiocarcinoma
,
esophageal squamous cell carcinoma
,
biliary tract neoplasms
,
gliosarcoma
,
t-cell lymphoma
,
t-cell lymphoma peripheral
,
kidney neoplasms
,
prostatic neoplasms
,
mantle-cell lymphoma
,
pancreatic ductal carcinoma
,
urethral neoplasms
,
ureteral neoplasms
,
neoplasms by histologic type
,
skin neoplasms
,
b-cell lymphoma marginal zone
,
castration-resistant prostatic neoplasms
,
nasopharyngeal neoplasms
,
leukemia
,
pelvic neoplasms
,
uveal melanoma
,
mouth neoplasms
,
oropharyngeal neoplasms
,
glandular and epithelial neoplasms
,
hypopharyngeal neoplasms
,
endometrioid carcinoma
,
t-cell lymphoma cutaneous
,
oncogenes
,
waldenstrom macroglobulinemia
,
kidney diseases
,
osteosarcoma
,
invasive hydatidiform mole
,
laryngeal neoplasms
,
neuroendocrine tumors
,
myeloid leukemia acute
,
precursor cell lymphoblastic leukemia-lymphoma
,
central nervous system diseases
,
histiocytic sarcoma
,
follicular dendritic cell sarcoma
,
interdigitating dendritic cell sarcoma
,
gallbladder neoplasms
,
chronic kidney failure
,
uterine neoplasms
,
carcinosarcoma
,
mullerian mixed tumor
,
disease
,
nervous system diseases
,
nerve tissue neoplasms
,
neuroepithelial neoplasms
,
neuroectodermal tumors
,
bile duct neoplasms
,
chordoma
,
neoplasms by site
,
serous cystadenocarcinoma
,
acinar cell carcinoma
,
mycoses
,
sezary syndrome
,
mycosis fungoides
,
syndrome
,
hematologic diseases
,
bone marrow diseases
,
non-muscle invasive bladder neoplasms
,
unknown primary neoplasms
,
immunoblastic lymphadenopathy
,
enteropathy-associated t-cell lymphoma
,
cutaneous malignant melanoma
,
merkel cell carcinoma
,
vaccinia
,
x-linked bulbo-spinal atrophy
,
nasopharyngeal carcinoma
,
microsatellite repeats
,
astrocytoma
,
pancreatitis
,
multiple myeloma
,
plasma cell neoplasms
,
epstein-barr virus infections
,
local neoplasm recurrence
,
hypersensitivity
,
adenoviridae infections
,
gastrointestinal stromal tumors
,
male breast neoplasms
,
adenosquamous carcinoma
,
uveal neoplasms
,
non-small-cell lung carcinoma
,
melanoma
,
colorectal neoplasms
,
squamous cell carcinoma of head and neck
,
carcinoma
,
lung neoplasms
,
head and neck neoplasms
,
squamous cell carcinoma
,
ovarian neoplasms
,
renal cell carcinoma
,
triple negative breast neoplasms
,
adenocarcinoma
,
large b-cell lymphoma diffuse
,
stomach neoplasms
,
uterine cervical neoplasms
,
urinary bladder neoplasms
,
hodgkin disease
,
fallopian tube neoplasms
,
arthritis
,
endometrial neoplasms
,
b-cell chronic lymphocytic leukemia
,
small cell lung carcinoma
,
transitional cell carcinoma
,
urologic neoplasms
,
rectal neoplasms
,
psoriatic arthritis
,
colonic neoplasms
,
ovarian epithelial carcinoma
,
malignant mesothelioma
,
clostridium infections
,
juvenile arthritis
,
hepatitis
,
hepatitis a
,
inflammatory bowel diseases
,
peritoneal neoplasms
,
axial spondyloarthritis
,
chronic hepatitis c
,
respiratory syncytial virus infections
,
hepatitis b
,
whooping cough
,
myositis
,
dermatomyositis
,
inclusion body myositis
,
polymyositis
,
polymyalgia rheumatica
,
spondylarthropathies
,
spondylarthritis
,
von hippel-lindau disease
,
neoplasms
,
rheumatoid arthritis
,
psoriasis
,
crohn disease
,
ankylosing spondylitis
,
infections
,
ulcerative colitis
,
communicable diseases
,
colitis
,
ulcer
,
hiv infections
,
papillomavirus infections
,
hiv
,
acquired immunodeficiency syndrome
,
immunologic deficiency syndromes
,
papilloma
,
pneumococcal infections
,
prostatic intraepithelial neoplasia
,
carcinoma in situ
,
uterine cervical dysplasia
,
papillomavirus vaccines
,
dengue
,
hepatitis c
,
coronavirus infections
,
human influenza
,
vasculitis
,
anti-neutrophil cytoplasmic antibody-associated vasculitis
,
intestinal neoplasms
,
human papillomavirus recombinant vaccine quadrivalent types 6 11 16 18
,
agammaglobulinemia
,
common variable immunodeficiency
,
papillomaviridae
,
chronic renal insufficiency
,
flavivirus infections
,
fibrosis
,
inflammation
,
coinfection
,
hypertension
,
prediabetic state
,
hypercholesterolemia
,
cerebrovascular disorders
,
diabetes mellitus
,
coronary artery disease
,
peripheral arterial disease
,
overweight
,
healthy volunteers/patients
Ag013736
healthy volunteers/patients
,
stomach neoplasms
,
castration-resistant prostatic neoplasms
,
malnutrition
,
liver failure
,
hepatic insufficiency
,
esophageal neoplasms
,
transitional cell carcinoma
,
uterine cervical neoplasms
,
small cell lung carcinoma
,
merkel cell carcinoma
,
colorectal neoplasms
,
hepatocellular carcinoma
,
melanoma
,
lung neoplasms
,
liver neoplasms
,
glioblastoma
,
thyroid neoplasms
,
thyroid diseases
,
endometrial neoplasms
,
sarcoma
,
skin neoplasms
,
neoplasm metastasis
,
pheochromocytoma
,
paraganglioma
,
thrombosis
,
non-hodgkin lymphoma
,
multiple myeloma
,
alveolar soft part sarcoma
,
recurrence
,
adenoid cystic carcinoma
,
carcinoid tumor
,
adrenal cortex neoplasms
,
adrenocortical carcinoma
,
malignant mesothelioma
,
mesothelioma
,
hemangiosarcoma
,
adenocarcinoma
,
pancreatic neoplasms
,
breast neoplasms
,
leukemia
,
myelodysplastic syndromes
,
myeloid leukemia acute
,
myeloid leukemia
,
preleukemia
,
syndrome
,
renal cell carcinoma
,
carcinoma
,
neoplasms
,
kidney neoplasms
,
non-small-cell lung carcinoma
,
neuroendocrine tumors
,
pancreatic ductal carcinoma
,
ovarian neoplasms
,
neoadjuvant therapy
,
lymphoma
,
gastrointestinal stromal tumors
,
mantle-cell lymphoma
Mk3475
lung diseases
,
myelodysplastic syndromes
,
lymphoid leukemia
,
thoracic neoplasms
,
neurologic manifestations
,
papillomaviridae
,
pharmacokinetics
,
soft tissue neoplasms
,
precursor cell lymphoblastic leukemia-lymphoma
,
respiratory tract neoplasms
,
bronchogenic carcinoma
,
endocrine gland neoplasms
,
breast diseases
,
bronchial neoplasms
,
intraductal carcinoma noninfiltrating
,
laryngeal diseases
,
myoepithelioma
,
oligodendroglioma
,
oral administration
,
lymphoma
,
pancreatic neoplasms
,
sarcoma
,
brain neoplasms
,
castration-resistant prostatic neoplasms
,
large b-cell lymphoma diffuse
,
b-cell lymphoma
,
non-hodgkin lymphoma
,
follicular lymphoma
,
myeloid leukemia acute
,
leukemia
,
t-cell lymphoma
,
kidney neoplasms
,
neuroendocrine tumors
,
pancreatic ductal carcinoma
,
uveal neoplasms
,
glioma
,
invasive hydatidiform mole
,
colonic neoplasms
,
neuroendocrine carcinoma
,
t-cell lymphoma peripheral
,
uveal melanoma
,
thyroid neoplasms
,
myeloid leukemia
,
urethral neoplasms
,
uterine neoplasms
,
microsatellite instability
,
cutaneous malignant melanoma
,
gastrointestinal neoplasms
,
mouth neoplasms
,
oropharyngeal neoplasms
,
small cell carcinoma
,
b-cell lymphoma marginal zone
,
anus neoplasms
,
female genital neoplasms
,
hypersensitivity
,
thymoma
,
epstein-barr virus infections
,
microsatellite repeats
,
rectal neoplasms
,
hypopharyngeal neoplasms
,
salivary gland neoplasms
,
endometrioid carcinoma
,
vulvar neoplasms
,
mantle-cell lymphoma
,
waldenstrom macroglobulinemia
,
non-muscle invasive bladder neoplasms
,
penile neoplasms
,
neoplasms by histologic type
,
liposarcoma
,
b-cell chronic lymphocytic leukemia
,
t-cell lymphoma cutaneous
,
ureteral neoplasms
,
osteosarcoma
,
gliosarcoma
,
carcinosarcoma
,
thymus neoplasms
,
burkitt lymphoma
,
laryngeal neoplasms
,
disease
,
adenoid cystic carcinoma
,
meningioma
,
serous cystadenocarcinoma
,
glandular and epithelial neoplasms
,
male breast neoplasms
,
leiomyosarcoma
,
adenocarcinoma of lung
,
oncogenes
,
neurofibrosarcoma
,
nerve sheath neoplasms
,
mycosis fungoides
,
syndrome
,
pelvic neoplasms
,
central nervous system neoplasms
,
germ cell and embryonal neoplasms
,
digestive system neoplasms
,
basal cell carcinoma
,
reactive arthritis
,
astrocytoma
,
adenosquamous carcinoma
,
gestational trophoblastic disease
,
alveolar soft part sarcoma
,
biphenotypic leukemia acute
,
local neoplasm recurrence
,
sclerosis
,
chordoma
,
meningeal carcinomatosis
,
immunoblastic lymphadenopathy
,
enteropathy-associated t-cell lymphoma
,
vaccinia
,
carcinoma in situ
,
cervical intraepithelial neoplasia
,
uterine cervical dysplasia
,
squamous intraepithelial lesions of the cervix
,
disease progression
,
central nervous system diseases
,
extranodal nk-t-cell lymphoma
,
neoplasms by site
,
x-linked bulbo-spinal atrophy
,
malignant fibrous histiocytoma
,
nasopharyngeal carcinoma
,
virus diseases
,
viremia
,
unknown primary neoplasms
,
synovial sarcoma
,
point mutation
,
oral leukoplakia
,
leukoplakia
,
hematologic diseases
,
bone marrow diseases
,
mycoses
,
sezary syndrome
,
endoscopy
,
colonic diseases
,
histiocytic sarcoma
,
follicular dendritic cell sarcoma
,
interdigitating dendritic cell sarcoma
,
environmental biomarkers
,
circulating neoplastic cells
,
inflammatory breast neoplasms
,
meningeal neoplasms
,
intestinal neoplasms
,
nervous system neoplasms
,
kidney diseases
,
nervous system diseases
,
nerve tissue neoplasms
,
neuroepithelial neoplasms
,
neuroectodermal tumors
,
anaplastic thyroid carcinoma
,
thyroid diseases
,
adrenocortical carcinoma
,
carcinoid tumor
,
parotid neoplasms
,
mediastinal neoplasms
,
testicular neoplasms
,
male genital neoplasms
,
gastrointestinal stromal tumors
,
hairy cell leukemia
,
spinal cord neoplasms
,
acinar cell carcinoma
,
adenoviridae infections
,
hypoxia
,
hereditary breast and ovarian cancer syndrome
,
mullerian mixed tumor
,
basal cell neoplasms
,
urogenital neoplasms
,
male urogenital diseases
,
hemangiosarcoma
,
perivascular epithelioid cell neoplasms
,
neoplasms
,
carcinoma
,
lung neoplasms
,
breast neoplasms
,
triple negative breast neoplasms
,
colorectal neoplasms
,
renal cell carcinoma
,
squamous cell carcinoma
,
ovarian neoplasms
,
neoplasm metastasis
,
head and neck neoplasms
,
stomach neoplasms
,
urinary bladder neoplasms
,
adenocarcinoma
,
prostatic neoplasms
,
recurrence
,
liver neoplasms
,
hepatocellular carcinoma
,
esophageal neoplasms
,
endometrial neoplasms
,
uterine cervical neoplasms
,
transitional cell carcinoma
,
small cell lung carcinoma
,
hodgkin disease
,
urologic neoplasms
,
fallopian tube neoplasms
,
glioblastoma
,
multiple myeloma
,
squamous cell neoplasms
,
ovarian epithelial carcinoma
,
mesothelioma
,
biliary tract neoplasms
,
esophageal squamous cell carcinoma
,
cholangiocarcinoma
,
plasma cell neoplasms
,
skin neoplasms
,
malignant mesothelioma
,
peritoneal neoplasms
,
merkel cell carcinoma
,
nasopharyngeal neoplasms
,
bile duct neoplasms
,
gallbladder neoplasms
,
hematologic neoplasms
,
non-small-cell lung carcinoma
,
melanoma
,
squamous cell carcinoma of head and neck
Asn100
ventilator-associated pneumonia
,
pneumonia
,
staphylococcal pneumonia
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