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Alexion Pharmaceuticals
Alexion Pharmaceuticals
(ALXN)
Alexion Pharmaceuticals is an American pharmaceutical company headquartered in Boston, Massachusetts that specializes in orphan drugs to treat rare diseases. It became an independent subsidiary of AstraZeneca in 2021.
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Revenue by Drug
Marketed Drugs
Therapeutic Areas:
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Classification:
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Include Generics:
Trade Name
Drug Name
Approved
Patent Expires
Indication
Kanuma
Sebelipase alfa
2015-12-08
Inborn errors lipid metabolism
Soliris
Eculizumab
2007-03-16
Paroxysmal hemoglobinuria
,
Myasthenia gravis
,
Atypical hemolytic uremic syndrome
Strensiq
Asfotase alfa
2015-10-23
Hypophosphatasia
Ultomiris
Ravulizumab
2018-12-21
Paroxysmal hemoglobinuria
,
Atypical hemolytic uremic syndrome
Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Drug Name
Phase 1
Phase 2
Phase 3
Phase 4
Indication
Ravulizumab
healthy volunteers/patients
,
glomerulonephritis
,
lupus nephritis
,
pre-eclampsia
,
hemolysis
,
thrombotic microangiopathies
,
neuromyelitis optica
,
iga glomerulonephritis
,
syndrome
,
atypical hemolytic uremic syndrome
,
anemia
,
vascular diseases
,
hemolytic-uremic syndrome
,
azotemia
,
chronic renal insufficiency
,
proteinuria
,
acute kidney injury
,
respiratory distress syndrome
,
pneumonia
,
acute lung injury
,
viral pneumonia
,
lung injury
,
newborn respiratory distress syndrome
,
amyotrophic lateral sclerosis
,
motor neuron disease
,
sclerosis
,
recurrence
,
transverse myelitis
,
demyelinating diseases
,
optic neuritis
,
muscle weakness
,
dermatomyositis
,
cardiopulmonary bypass
,
heart diseases
,
kidney transplantation
,
delayed graft function
,
iga vasculitis
,
vasculitis
,
paroxysmal hemoglobinuria
,
hemoglobinuria
,
myasthenia gravis
,
covid-19
,
adrenal insufficiency
,
pregnancy
Asfotase alfa
hypophosphatasia
Sebelipase alfa
mucopolysaccharidosis iv
,
glycogen storage disease type ii
,
lysosomal storage diseases
,
gaucher disease
,
fabry disease
,
cholesterol ester storage disease
,
wolman disease
,
failure to thrive
Eculizumab
healthy volunteers/patients
,
liver diseases
,
end stage liver disease
,
kidney diseases
,
glomerulonephritis
,
membranoproliferative glomerulonephritis
,
pre-eclampsia
,
hellp syndrome
,
chronic kidney failure
,
vasculitis
,
anti-neutrophil cytoplasmic antibody-associated vasculitis
,
pregnancy rate
,
sars-cov-2
,
multiple organ failure
,
diabetes mellitus
,
thrombocytopenia
,
complement activation
,
psychology rejection
,
renal insufficiency
,
wounds and injuries
,
reperfusion injury
,
chronic renal insufficiency
,
hemolytic anemia autoimmune
,
death
,
antiphospholipid syndrome
,
macular degeneration
,
geographic atrophy
,
asthma
,
dermatomyositis
,
autoimmune diseases
,
anti-glomerular basement membrane disease
,
neuromyelitis optica
,
myasthenia gravis
,
kidney transplantation
,
muscle weakness
,
vascular diseases
,
thrombotic microangiopathies
,
guillain-barre syndrome
,
delayed graft function
,
anemia
,
escherichia coli infections
,
left ventricular dysfunction
,
ventricular dysfunction
,
shiga-toxigenic escherichia coli
,
leukemia
,
emergencies
,
malignant hypertension
,
hypertensive crisis
,
phenylketonurias
,
paroxysmal hemoglobinuria
,
hemoglobinuria
,
hemolysis
,
syndrome
,
hemolytic-uremic syndrome
,
atypical hemolytic uremic syndrome
,
azotemia
,
covid-19
,
coronavirus infections
,
respiratory distress syndrome
,
pneumonia
,
acute lung injury
,
hypophosphatasia
,
severe acute respiratory syndrome
,
viral pneumonia
,
lung injury
,
newborn respiratory distress syndrome
,
coronavirus
,
protein-losing enteropathies
,
intestinal diseases
,
hemophilia b
,
lymphangiectasis
,
intestinal lymphangiectasis
,
pregnancy
,
disease progression
,
intestinal obstruction
,
sinusitis
,
allergic fungal sinusitis
,
rhinosinusitis
,
observation
Danicopan
healthy volunteers/patients
,
hepatic insufficiency
,
renal insufficiency
,
glomerulonephritis
,
membranoproliferative glomerulonephritis
,
covid-19
,
geographic atrophy
,
paroxysmal hemoglobinuria
,
hemoglobinuria
,
hemolysis
,
anemia
Mycophenolate sodium
autoimmune diseases
,
chronic kidney failure
,
systemic scleroderma
,
lung diseases
,
interstitial lung diseases
,
localized scleroderma
,
diffuse scleroderma
,
psychology rejection
,
renal insufficiency
,
diabetic nephropathies
,
hypertension
,
kidney diseases
,
iga glomerulonephritis
,
renal hypertension
,
diabetes mellitus
,
lupus nephritis
,
kidney transplantation
,
systemic lupus erythematosus
,
nephrotic syndrome
,
pemphigus
,
nephritis
Benzodiazepine
parkinson disease
Benzimidazole
healthy volunteers/patients
,
rheumatoid arthritis
,
arthritis
,
drug interactions
,
leukemia
,
b-cell chronic lymphocytic leukemia
,
lymphoid leukemia
,
alzheimer disease
,
prostatic neoplasms
,
carcinoma
,
small cell carcinoma
,
neuroendocrine carcinoma
,
hodgkin disease
,
lymphoma
,
neoplasms
,
t-cell lymphoma
,
t-cell lymphoma peripheral
,
hematoma
,
graft rejection
,
atrial fibrillation
,
thrombosis
,
embolism
Cerdulatinib
b-cell chronic lymphocytic leukemia
,
leukemia
,
hodgkin disease
,
b-cell lymphoma
,
t-cell lymphoma cutaneous
,
bronchiolitis obliterans syndrome
,
vitiligo
,
t-cell lymphoma
,
follicular lymphoma
,
lymphoma
,
large-cell lymphoma anaplastic
,
t-cell lymphoma peripheral
,
non-hodgkin lymphoma
Pexelizumab
coronary artery disease
,
cardiopulmonary bypass
,
coronary artery bypass
Tenofovir
hepatitis b
,
chronic hepatitis b
,
hepatitis
,
chronic hepatitis
,
hepatitis a
Choline alfoscerate
alzheimer disease
Somatostatin
type 2 diabetes mellitus
,
glucose metabolism disorders
,
metabolic diseases
,
diabetes mellitus
,
endocrine system diseases
,
neoplasms
,
neuroendocrine tumors
Doconexent
sepsis
,
toxemia
Lornoxicam
neuroblastoma
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3
4
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