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Alexion Pharmaceuticals
Alexion Pharmaceuticals
(ALXN)
Alexion Pharmaceuticals is an American pharmaceutical company headquartered in Boston, Massachusetts that specializes in orphan drugs to treat rare diseases. It became an independent subsidiary of AstraZeneca in 2021.
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Trade Name
Drug Name
Approved
Patent Expires
Indication
Kanuma
Sebelipase alfa
2015-12-08
Inborn errors lipid metabolism
Soliris
Eculizumab
2007-03-16
Paroxysmal hemoglobinuria
,
Myasthenia gravis
,
Atypical hemolytic uremic syndrome
Strensiq
Asfotase alfa
2015-10-23
Hypophosphatasia
Ultomiris
Ravulizumab
2018-12-21
Paroxysmal hemoglobinuria
,
Atypical hemolytic uremic syndrome
Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Drug Name
Phase 1
Phase 2
Phase 3
Phase 4
Indication
Ravulizumab
healthy volunteers/patients
,
lupus nephritis
,
hemolysis
,
myasthenia gravis
,
kidney diseases
,
neuromyelitis optica
,
muscle weakness
,
vascular diseases
,
thrombotic microangiopathies
,
iga glomerulonephritis
,
syndrome
,
hemolytic-uremic syndrome
,
atypical hemolytic uremic syndrome
,
nephritis
,
azotemia
,
covid-19
,
respiratory distress syndrome
,
pneumonia
,
acute lung injury
,
viral pneumonia
,
lung injury
,
newborn respiratory distress syndrome
,
amyotrophic lateral sclerosis
,
motor neuron disease
,
sclerosis
,
dermatomyositis
,
chronic renal insufficiency
,
cardiopulmonary bypass
,
heart diseases
,
kidney transplantation
,
delayed graft function
,
iga vasculitis
,
vasculitis
,
purpura
,
paroxysmal hemoglobinuria
,
hemoglobinuria
,
pregnancy
Asfotase alfa
hypophosphatasia
Sebelipase alfa
fabry disease
,
cholesterol ester storage disease
,
wolman disease
,
failure to thrive
Eculizumab
glomerulonephritis
,
membranoproliferative glomerulonephritis
,
liver diseases
,
end stage liver disease
,
azotemia
,
kidney transplantation
,
kidney diseases
,
vasculitis
,
anti-neutrophil cytoplasmic antibody-associated vasculitis
,
pre-eclampsia
,
pregnancy rate
,
hellp syndrome
,
complement activation
,
chronic renal insufficiency
,
hemolytic anemia autoimmune
,
death
,
macular degeneration
,
geographic atrophy
,
asthma
,
hemolysis
,
syndrome
,
hemolytic-uremic syndrome
,
atypical hemolytic uremic syndrome
,
myasthenia gravis
,
neuromyelitis optica
,
muscle weakness
,
delayed graft function
,
guillain-barre syndrome
,
left ventricular dysfunction
,
ventricular dysfunction
,
escherichia coli infections
,
shiga-toxigenic escherichia coli
,
phenylketonurias
,
paroxysmal hemoglobinuria
,
hemoglobinuria
,
covid-19
,
hypophosphatasia
,
respiratory distress syndrome
,
pneumonia
,
acute lung injury
,
viral pneumonia
,
lung injury
,
newborn respiratory distress syndrome
,
pregnancy
,
disease progression
Danicopan
healthy volunteers/patients
,
liver diseases
,
hepatic insufficiency
,
renal insufficiency
,
glomerulonephritis
,
membranoproliferative glomerulonephritis
,
macular degeneration
,
geographic atrophy
,
atrophy
,
paroxysmal hemoglobinuria
,
hemoglobinuria
,
hemolysis
Mycophenolate sodium
healthy volunteers/patients
Mycophenolic acid
precursor cell lymphoblastic leukemia-lymphoma
,
lymphoid leukemia
,
neoplasms
,
lymphoma
,
hematologic neoplasms
,
liver transplantation
,
myelodysplastic syndromes
,
heart transplantation
,
non-hodgkin lymphoma
,
multiple myeloma
,
b-cell chronic lymphocytic leukemia
,
bcr-abl positive chronic myelogenous leukemia
,
hodgkin disease
,
preleukemia
,
liver diseases
,
anemia
,
aplastic anemia
,
leukemia
,
myeloid leukemia acute
,
myeloid leukemia
,
diabetic nephropathies
,
type 1 diabetes mellitus
,
kidney transplantation
,
graft rejection
,
chronic kidney failure
,
kidney diseases
,
cytomegalovirus
,
death
,
transplantation
,
diabetes mellitus
Iron dextran
leukemia
,
myelodysplastic syndromes
,
myelomonocytic leukemia chronic
,
preleukemia
,
syndrome
Cerdulatinib
non-hodgkin lymphoma
,
b-cell chronic lymphocytic leukemia
,
leukemia
,
lymphoma
,
t-cell lymphoma
,
hodgkin disease
,
follicular lymphoma
,
b-cell lymphoma
,
lymphoid leukemia
Lampalizumab
leukemia
,
precursor cell lymphoblastic leukemia-lymphoma
,
philadelphia chromosome
,
lymphoid leukemia
Pexelizumab
myocardial infarction
,
infarction
,
inferior wall myocardial infarction
,
coronary artery disease
,
cardiopulmonary bypass
,
coronary artery bypass
Tenofovir
healthy volunteers/patients
,
virus diseases
,
herpesviridae infections
,
leukoencephalopathies
,
progressive multifocal leukoencephalopathy
,
infections
,
chronic hepatitis d
,
hepatitis d
,
acquired immunodeficiency syndrome
,
hepatitis
,
hepatitis a
,
hepatitis b
,
hiv infections
,
chronic hepatitis b
,
chronic hepatitis
Choline alfoscerate
healthy volunteers/patients
,
cardiovascular diseases
,
recurrence
,
pregnancy
,
child development
,
diet therapy
,
male infertility
,
infertility
,
esophageal neoplasms
,
immunization
,
non-hodgkin lymphoma
,
lymphoma
,
hodgkin disease
,
large b-cell lymphoma diffuse
,
food diet and nutrition
,
lymphangioleiomyomatosis
,
cannabis
,
malaria
,
pharmacokinetics
,
carcinoma
,
hepatocellular carcinoma
,
liver neoplasms
,
fetal alcohol spectrum disorders
,
breast neoplasms
,
cystic fibrosis
,
covid-19
,
leukemia
,
schizophrenia
,
triple negative breast neoplasms
,
substance-related disorders
,
cognition disorders
,
neurodevelopmental disorders
,
marijuana abuse
,
heart valve diseases
,
presbyopia
,
hemophilia a
,
myeloid leukemia acute
,
megakaryoblastic leukemia acute
,
monocytic leukemia acute
,
myelomonocytic leukemia acute
,
myeloid leukemia
,
erythroblastic leukemia acute
,
hypersensitivity
,
macular edema
,
edema
,
reperfusion injury
,
myocardial reperfusion injury
,
sepsis
,
toxemia
,
exocrine pancreatic insufficiency
,
ataxia
,
tremor
,
cerebellar ataxia
,
lung injury
,
autism spectrum disorder
,
pervasive child development disorders
,
prostatic neoplasms
,
syndrome
,
liver diseases
,
hyperparathyroidism
,
hypertriglyceridemia
,
obesity
,
non-alcoholic fatty liver disease
,
fibrosis
,
prader-willi syndrome
,
hepatolenticular degeneration
,
coronary artery disease
,
open-angle glaucoma
,
premature birth
,
heart diseases
,
primary hyperparathyroidism
,
ischemic stroke
,
adenoma
,
parathyroid neoplasms
,
coronary disease
,
myocardial ischemia
,
metabolic syndrome
,
adenocarcinoma
,
choline deficiency
,
hypoxia
,
diabetic neuropathies
,
multiple myeloma
,
plasma cell neoplasms
,
brain diseases
,
brain ischemia
,
brain hypoxia-ischemia
,
intestinal failure
,
severe acute malnutrition
,
castration-resistant prostatic neoplasms
,
parathyroid diseases
,
rapid sequence induction and intubation
,
hyperhomocysteinemia
,
liver cirrhosis
,
atherosclerotic plaque
,
mania
,
anemia
,
iron-deficiency anemia
,
iron deficiencies
,
neuroprotection
,
cognitive dysfunction
,
malnutrition
,
alzheimer disease
,
dyslipidemias
,
glaucoma
,
fatty liver
,
ischemia
,
neoplasms
,
cerebral infarction
,
infarction
,
diabetes mellitus
,
brain injuries
,
stroke
,
wounds and injuries
,
traumatic brain injuries
,
asthma
,
optic nerve diseases
,
inflammation
,
septic shock
,
shock
,
atherosclerosis
,
bipolar disorder
,
peripheral nervous system diseases
,
ischemic optic neuropathy
,
alcoholism
,
myocardial infarction
,
chemical and drug induced liver injury
,
autistic disorder
,
cocaine-related disorders
,
dementia
,
type 2 diabetes mellitus
,
alcohol drinking
,
microvascular angina
,
asperger syndrome
,
delirium
,
psychotic disorders
,
hepatitis
,
cholestasis
,
hepatitis a
,
alcoholic hepatitis
,
postoperative pain
,
neural conduction
,
carotid artery diseases
,
respiratory aspiration
,
hypotension
,
laparotomy
,
emergencies
,
heart disease risk factors
,
brain neoplasms
,
depression
,
depressive disorder
,
neoplasm metastasis
,
neuralgia
,
lung neoplasms
,
heart failure
,
thyroid neoplasms
,
neuroendocrine carcinoma
,
thyroid diseases
,
major depressive disorder
,
postmenopause
,
anxiety disorders
,
melanoma
,
overweight
,
prostatic hyperplasia
,
neuroendocrine tumors
,
hyperplasia
,
pain
,
body weight
,
body weight changes
,
myalgia
,
energy drinks
,
non-small-cell lung carcinoma
,
infant nutrition disorders
,
alcoholic liver diseases
,
glioma
,
papillary thyroid cancer
,
coronary stenosis
,
bone neoplasms
,
bone marrow diseases
,
thyroid nodule
,
erdheim-chester disease
,
histiocytosis
,
langerhans-cell histiocytosis
,
tourette syndrome
,
myasthenia gravis
,
muscle weakness
,
amphetamine-related disorders
,
lactation
,
liver transplantation
,
erythema
,
gestational diabetes
,
metabolism
,
anxiety
,
neurodegenerative diseases
,
breast feeding
,
kinetics
,
carotid stenosis
,
irritable bowel syndrome
,
positron-emission tomography
,
total parenteral nutrition
,
endometrial neoplasms
,
uterine cervical neoplasms
,
disease
,
lymphatic metastasis
,
muscle strength
,
rhabdomyolysis
,
uveal neoplasms
,
urologic neoplasms
,
amyotrophic lateral sclerosis
,
muscle spasticity
,
motor neuron disease
,
hereditary spastic paraplegia
,
sclerosis
,
paraplegia
,
postpartum depression
,
hypertension
,
hypercholesterolemia
,
mycoses
,
infections
,
communicable diseases
,
onychomycosis
,
essential hypertension
,
arthritis
,
chronic pain
,
fibromyalgia
,
neurotoxicity syndromes
,
peripheral nerve injuries
,
nerve degeneration
,
organophosphate poisoning
,
neuroinflammatory diseases
,
obstetrical anesthesia
,
emotional regulation
,
executive function
,
cold temperature
,
gastrointestinal diseases
,
digestive system diseases
,
kwashiorkor
,
oral ulcer
,
cognition
,
exercise tolerance
,
therapeutic chemoembolization
,
head and neck neoplasms
,
gastrointestinal neoplasms
,
urogenital neoplasms
,
skin neoplasms
,
intestinal neoplasms
,
thoracoscopy
,
exfoliation syndrome
,
menopause
Doconexent
type 2 diabetes mellitus
,
diabetes mellitus
Lornoxicam
female genital neoplasms
,
nervous system diseases
,
adrenocortical carcinoma
,
pregnancy
,
antiphospholipid syndrome
,
juvenile arthritis
,
analgesia
,
gastrointestinal stromal tumors
,
immunoglobulin g4-related disease
,
bile duct neoplasms
,
pharmacokinetics
,
pheochromocytoma
,
paraganglioma
,
deltaretrovirus infections
,
htlv-i infections
,
composite lymphoma
,
eyelid diseases
,
osteogenesis imperfecta
,
neuroepithelial neoplasms
,
pharyngeal neoplasms
,
male genital neoplasms
,
poems syndrome
,
smooth muscle tumor
,
papillary thyroid cancer
,
medullary carcinoma
,
ganglioglioma
,
ischemia
,
peripheral arterial disease
,
peripheral vascular diseases
,
carcinoid tumor
,
skin diseases
,
adrenal cortex neoplasms
,
papillomaviridae
,
papilloma
,
gout
,
ovarian diseases
,
abdominal neoplasms
,
lymphocytosis
,
small cell carcinoma
,
neuromuscular manifestations
,
demyelinating diseases
,
cns demyelinating autoimmune diseases
,
transplantation tolerance
,
stomach neoplasms
,
liver neoplasms
,
prostatic neoplasms
,
hepatocellular carcinoma
,
uterine cervical neoplasms
,
skin neoplasms
,
glioblastoma
,
glioma
,
prolymphocytic leukemia
,
mesothelioma
,
esophageal neoplasms
,
head and neck neoplasms
,
squamous cell neoplasms
,
malignant mesothelioma
,
myeloid leukemia accelerated phase
,
adult t-cell leukemia-lymphoma
,
residual neoplasm
,
blast crisis
,
mycoses
,
t-cell lymphoma cutaneous
,
myxoid liposarcoma
,
plasma cell leukemia
,
mycosis fungoides
,
aids-related lymphoma
,
lymphomatoid granulomatosis
,
castration-resistant prostatic neoplasms
,
crohn disease
,
chronic granulomatous disease
,
anus neoplasms
,
colonic neoplasms
,
invasive hydatidiform mole
,
rheumatoid arthritis
,
arthritis
,
cholangiocarcinoma
,
diffuse intrinsic pontine glioma
,
nasopharyngeal carcinoma
,
nasopharyngeal neoplasms
,
rectal neoplasms
,
prolymphocytic leukemia t-cell
,
thyroid neoplasms
,
astrocytoma
,
sezary syndrome
,
endometrial neoplasms
,
reactive arthritis
,
gastrointestinal neoplasms
,
myasthenia gravis
,
precancerous conditions
,
intestinal neoplasms
,
uveal neoplasms
,
primary immunodeficiency diseases
,
muscular diseases
,
urologic neoplasms
,
merkel cell carcinoma
,
thymus neoplasms
,
hairy cell leukemia
,
intraocular lymphoma
,
metabolic diseases
,
neuroendocrine tumors
,
kidney transplantation
,
granuloma
,
thyroid diseases
,
oropharyngeal neoplasms
,
pancreatic ductal carcinoma
,
disease progression
,
serous cystadenocarcinoma
,
muscle weakness
,
immunosuppression therapy
,
common variable immunodeficiency
,
polycythemia vera
,
polycythemia
,
bone fractures
,
vulvar neoplasms
,
penile neoplasms
,
castleman disease
,
primary effusion lymphoma
,
desmoplastic small round cell tumor
,
thymoma
,
wiskott-aldrich syndrome
,
intestinal diseases
,
healthy volunteers/patients
,
hepatitis b
,
precursor b-cell lymphoblastic leukemia-lymphoma
,
autoimmune diseases of the nervous system
,
large granular lymphocytic leukemia
,
vaginal neoplasms
,
gliosarcoma
,
germinoma
,
adenocarcinoma of lung
,
pinealoma
,
iga vasculitis
,
hypertension
,
gata2 deficiency
,
hepatoblastoma
,
essential thrombocythemia
,
thrombocytosis
,
x-linked combined immunodeficiency diseases
,
adenosquamous carcinoma
,
vitamin d deficiency
,
digestive system neoplasms
,
epstein-barr virus infections
,
pure red-cell aplasia
,
hemolytic anemia autoimmune
,
hemolytic anemia
,
chronic inflammatory demyelinating polyradiculoneuropathy
,
type 1 diabetes mellitus
,
oligodendroglioma
,
cord blood stem cell transplantation
,
graft rejection
,
microsatellite instability
,
transitional cell carcinoma
,
carcinoma in situ
,
hemangiosarcoma
,
malignant pleural effusion
,
endodermal sinus tumor
,
cytopenia
,
prolymphocytic leukemia b-cell
,
cardiovascular diseases
,
hepatitis
,
liver transplantation
,
encephalitis
,
meningioma
,
metabolic syndrome
,
autoimmune lymphoproliferative syndrome
,
pulmonary hypertension
,
epidermolysis bullosa
,
neuroendocrine carcinoma
,
mucopolysaccharidosis vi
,
mucopolysaccharidosis i
,
alpha-mannosidosis
,
mannosidase deficiency diseases
,
inborn genetic diseases
,
glandular and epithelial neoplasms
,
urogenital neoplasms
,
endocrine gland neoplasms
,
stiff-person syndrome
,
immunoproliferative disorders
,
hemolysis
,
neoplasms by histologic type
,
myoepithelioma
,
immunotherapy
,
cell- and tissue-based therapy
,
adoptive immunotherapy
,
monoclonal gammopathy of undetermined significance
,
brain diseases
,
endometrioid carcinoma
,
cystadenocarcinoma
,
breast carcinoma in situ
,
teratoma
,
choriocarcinoma
,
embryonal carcinoma
,
cytokine release syndrome
,
homologous transplantation
,
smoldering multiple myeloma
,
fatigue
,
treatment refusal
,
pain
,
focal segmental glomerulosclerosis
,
metabolic brain diseases
,
hiv seropositivity
,
leukopenia
,
mastocytosis
,
mucopolysaccharidosis vii
,
aspartylglucosaminuria
,
sphingolipidoses
,
nijmegen breakage syndrome
,
lymphatic diseases
,
thrombasthenia
,
polyneuropathies
,
disease
,
biliary tract neoplasms
,
alzheimer disease
,
polyradiculoneuropathy
,
papillomavirus infections
,
experimental melanoma
,
mesenchymal stem cell transplantation
,
migraine disorders
,
radiotherapy
,
hiv-2
,
central nervous system vasculitis
,
chordoma
,
uterine neoplasms
,
clear cell adenocarcinoma
,
acinar cell carcinoma
,
lobular carcinoma
,
thoracic neoplasms
,
clonal hematopoiesis
,
aneuploidy
,
autologous transplantation
,
non-gestational choriocarcinoma
,
antineoplastic combined chemotherapy protocols
,
appendiceal neoplasms
,
neoplasms by site
,
myc genes
,
congenital abnormalities
,
gene rearrangement
,
conjunctival neoplasms
,
deficiency diseases
,
pneumocephalus
,
mast-cell leukemia
,
necrosis
,
supratentorial neoplasms
,
basal cell carcinoma
,
basal cell nevus syndrome
,
monosomy
,
leukemia myeloid chronic atypical bcr-abl negative
,
graft survival
,
neutrophilic leukemia chronic
,
hypereosinophilic syndrome
,
eosinophilic leukemia acute
,
job syndrome
,
mucopolysaccharidosis ii
,
peroxisomal disorders
,
systemic mastocytosis
,
erythema
,
combination drug therapy
,
hereditary breast and ovarian cancer syndrome
,
prosthesis failure
,
pleural diseases
,
heart diseases
,
mucinous cystadenocarcinoma
,
hyperglycemia
,
chronic fatigue syndrome
,
myalgia
,
encephalomyelitis
,
metaplasia
,
frontotemporal dementia
,
type b niemann-pick disease
,
primary progressive aphasia
,
mucolipidoses
,
adenocarcinoma in situ
,
experimental neoplasms
,
malnutrition
,
depression
,
gastrointestinal diseases
,
diarrhea
,
felty syndrome
,
radiation effects
,
bunion
,
orthopedic procedures
,
sarcoidosis
,
gallbladder neoplasms
,
oral lichen planus
,
unilateral breast neoplasms
,
vulvar diseases
,
cervical intraepithelial neoplasia
,
uterine cervical dysplasia
,
anaplastic thyroid carcinoma
,
giant cell tumor of bone
,
giant cell tumors
,
squamous intraepithelial lesions
,
headache
,
intractable pain
,
metabolic brain diseases inborn
,
antibiotic prophylaxis
,
measles
,
ischemic stroke
,
stroke
,
cerebral infarction
,
paresis
,
infarction
,
paralysis
,
heterologous transplantation
,
pulpitis
,
endodontics
,
eyelid neoplasms
,
blood protein disorders
,
respiratory aspiration
,
cystinosis
,
aneurysm
,
chimera
,
fasting
,
extranodal extension
,
li-fraumeni syndrome
,
p53 genes
,
polymyositis
,
olfactory esthesioneuroblastoma
,
splenomegaly
,
invasive fungal infections
,
duodenal neoplasms
,
probiotics
,
pseudomyxoma peritonei
,
behavior therapy
,
neoplasms
,
myeloid leukemia acute
,
myeloid leukemia
,
hematologic neoplasms
,
melanoma
,
carcinoma
,
bcr-abl positive chronic myelogenous leukemia
,
ovarian neoplasms
,
myeloproliferative disorders
,
lung neoplasms
,
non-small-cell lung carcinoma
,
neoplasm metastasis
,
pancreatic neoplasms
,
ovarian epithelial carcinoma
,
precursor t-cell lymphoblastic leukemia-lymphoma
,
colorectal neoplasms
,
b-cell lymphoma marginal zone
,
myelodysplastic-myeloproliferative diseases
,
renal cell carcinoma
,
central nervous system neoplasms
,
adenocarcinoma
,
biphenotypic leukemia acute
,
myelomonocytic leukemia chronic
,
ewing sarcoma
,
primary myelofibrosis
,
fallopian tube neoplasms
,
kidney neoplasms
,
autoimmune diseases
,
sickle cell anemia
,
nervous system neoplasms
,
brain neoplasms
,
hematologic diseases
,
squamous cell carcinoma
,
t-cell leukemia
,
acute disease
,
osteosarcoma
,
squamous cell carcinoma of head and neck
,
b-cell leukemia
,
multiple sclerosis
,
inflammatory breast neoplasms
,
large-cell lymphoma immunoblastic
,
immunologic deficiency syndromes
,
neuroectodermal tumors
,
plasmablastic lymphoma
,
fanconi anemia
,
synovial sarcoma
,
pancytopenia
,
myositis
,
ependymoma
,
liposarcoma
,
bone marrow failure disorders
,
fanconi syndrome
,
extranodal nk-t-cell lymphoma
,
peritoneal neoplasms
,
thrombocytopenia
,
myelomonocytic leukemia acute
,
cutaneous malignant melanoma
,
refractory anemia with excess of blasts
,
retinoblastoma
,
small cell lung carcinoma
,
immune system diseases
,
drug-related side effects and adverse reactions
,
embryonal rhabdomyosarcoma
,
classical conditioning
,
rhabdoid tumor
,
primitive neuroectodermal tumors peripheral
,
pathologic complete response
,
paroxysmal hemoglobinuria
,
refractory anemia
,
alveolar rhabdomyosarcoma
,
cerebrotendinous xanthomatosis
,
xanthomatosis
,
hemoglobinopathies
,
thrombocytopenic purpura idiopathic
,
bone marrow transplantation
,
ductal carcinoma breast
,
second primary neoplasms
,
hemoglobinuria
,
hemophagocytic lymphohistiocytosis
,
stem cell transplantation
,
paraproteinemias
,
chronic kidney failure
,
histiocytosis
,
clear cell sarcoma
,
testicular neoplasms
,
peripheral blood stem cell transplantation
,
relapsing-remitting multiple sclerosis
,
purpura
,
mucinous adenocarcinoma
,
ganglioneuroblastoma
,
chemotherapy-induced febrile neutropenia
,
peripheral nervous system diseases
,
cognitive dysfunction
,
erythroblastic leukemia acute
,
phenylketonurias
,
langerhans-cell histiocytosis
,
bone neoplasms
,
chondrosarcoma
,
fibrosarcoma
,
benign fibrous histiocytoma
,
histiocytoma
,
brain stem neoplasms
,
chronic progressive multiple sclerosis
,
neuromyelitis optica
,
megakaryoblastic leukemia acute
,
diamond-blackfan anemia
,
pulmonary fibrosis
,
drug therapy
,
soft tissue neoplasms
,
carcinosarcoma
,
monocytic leukemia acute
,
malaria
,
infertility
,
promyelocytic leukemia acute
,
arteritis
,
takayasu arteritis
,
aortic arch syndromes
,
severe combined immunodeficiency
,
chediak-higashi syndrome
,
osteopetrosis
,
nephrotic syndrome
,
nephrosis
,
thrombocytopenic purpura
,
down syndrome
,
inflammation
,
mouth neoplasms
,
malignant fibrous histiocytoma
,
mesenchymal chondrosarcoma
,
behcet syndrome
,
breast diseases
,
ductal carcinoma
,
neurotoxicity syndromes
,
fever
,
inborn errors metabolism
,
mucopolysaccharidoses
,
fucosidosis
,
globoid cell leukodystrophy
,
adrenoleukodystrophy
,
dyskeratosis congenita
,
shwachman-diamond syndrome
,
pulmonary blastoma
,
trophoblastic neoplasms
,
therapeutics
,
alveolar soft part sarcoma
,
neurofibrosarcoma
,
nerve sheath neoplasms
,
mullerian mixed tumor
,
chemotherapy-related cognitive impairment
,
ocular motility disorders
,
myoclonus
,
opsoclonus-myoclonus syndrome
,
mucositis
,
choroid plexus neoplasms
,
gestational trophoblastic disease
,
metachromatic leukodystrophy
,
idiopathic pulmonary fibrosis
,
unknown primary neoplasms
,
eosinophilic granuloma
,
tuberculosis
,
niemann-pick diseases
,
type a niemann-pick disease
,
wolman disease
,
type c niemann-pick disease
,
pick disease of the brain
,
connective tissue diseases
,
whole-body irradiation
,
hyperthermia
,
circulating neoplastic cells
,
anti-glomerular basement membrane disease
,
adolescent development
,
hematopoietic stem cell mobilization
,
postoperative complications
,
bone marrow diseases
,
leiomyosarcoma
,
perivascular epithelioid cell neoplasms
,
glomus tumor
,
granular cell tumor
,
cognition
,
scleritis
,
hearing loss
,
sensorineural hearing loss
,
lipoid nephrosis
,
adjuvant chemotherapy
,
bullous pemphigoid
,
benign mucous membrane pemphigoid
,
meningeal tuberculosis
,
meningitis
,
arachnoiditis
,
retinal neoplasms
,
mesenchymoma
,
inguinal hernia
,
hernia
,
mixed connective tissue disease
,
neuronal ceroid-lipofuscinoses
,
tay-sachs disease
,
sandhoff disease
,
gm1 gangliosidosis
,
gaucher disease
,
gangliosidoses
,
stomatitis
,
acute kidney injury
,
rheumatic diseases
,
collagen diseases
,
warts
,
condylomata acuminata
,
thrombosis
,
positron-emission tomography
,
hemorrhoids
,
lymphoma
,
leukemia
,
breast neoplasms
,
precursor cell lymphoblastic leukemia-lymphoma
,
non-hodgkin lymphoma
,
lymphoid leukemia
,
multiple myeloma
,
b-cell lymphoma
,
plasma cell neoplasms
,
large b-cell lymphoma diffuse
,
myelodysplastic syndromes
,
b-cell chronic lymphocytic leukemia
,
preleukemia
,
syndrome
,
recurrence
,
hodgkin disease
,
triple negative breast neoplasms
,
follicular lymphoma
,
mantle-cell lymphoma
,
t-cell lymphoma
,
sarcoma
,
neuroblastoma
,
graft vs host disease
,
t-cell lymphoma peripheral
,
anemia
,
plasmacytoma
,
aplastic anemia
,
systemic lupus erythematosus
,
burkitt lymphoma
,
nephritis
,
myelomonocytic leukemia juvenile
,
sclerosis
,
systemic scleroderma
,
lupus nephritis
,
waldenstrom macroglobulinemia
,
hematopoietic stem cell transplantation
,
diffuse scleroderma
,
vasculitis
,
rhabdomyosarcoma
,
large-cell lymphoma anaplastic
,
kidney diseases
,
medulloblastoma
,
neutropenia
,
philadelphia chromosome
,
germ cell and embryonal neoplasms
,
lymphoproliferative disorders
,
amyloidosis
,
myeloid leukemia chronic-phase
,
anti-neutrophil cytoplasmic antibody-associated vasculitis
,
primitive neuroectodermal tumors
,
vomiting
,
immunoblastic lymphadenopathy
,
membranous glomerulonephritis
,
osteoporosis
,
hiv infections
,
immunoglobulin light-chain amyloidosis
,
nausea
,
renal insufficiency
,
male breast neoplasms
,
aggression
,
granulomatosis with polyangiitis
,
thalassemia
,
wilms tumor
,
cardiotoxicity
,
enteropathy-associated t-cell lymphoma
,
neoadjuvant therapy
,
microscopic polyangiitis
,
iga glomerulonephritis
,
glomerulonephritis
,
systemic vasculitis
,
lung diseases
,
localized scleroderma
,
beta-thalassemia
,
infections
,
acquired immunodeficiency syndrome
,
interstitial lung diseases
,
urinary bladder neoplasms
,
diabetes mellitus
,
hiv
,
churg-strauss syndrome
,
metabolic bone diseases
,
pemphigus
,
sjogren's syndrome
,
myeloid sarcoma
,
bronchiolitis obliterans syndrome
,
postoperative pain
,
postmenopausal osteoporosis
,
febrile neutropenia
,
type 2 diabetes mellitus
,
communicable diseases
,
hemophilia a
,
fibrosis
,
polyarteritis nodosa
,
obesity
,
panniculitis
,
menopause
,
dermatomyositis
,
human herpesvirus 8
,
uveitis
,
virus diseases
,
glycogen storage disease type ii
,
edema
,
pneumonia
,
acute coronary syndrome
,
mediastinal neoplasms
,
glycogen storage disease type iii
,
glycogen storage disease
,
kaposi sarcoma
,
intravesical administration
,
cystitis
,
non-muscle invasive bladder neoplasms
,
retroperitoneal fibrosis
,
acute pain
,
trismus
,
arthralgia
,
bone resorption
,
knee osteoarthritis
,
osteoarthritis
,
inflammatory bowel diseases
,
hemoglobin sc disease
,
type 1 hyper-igm immunodeficiency syndrome
,
hyper-igm immunodeficiency syndrome
,
alopecia areata
,
alopecia
,
bone diseases
,
periodontitis
,
cytomegalovirus infections
,
hemoglobin c disease
,
taste disorders
,
dysgeusia
,
ageusia
,
ataxia
,
ataxia telangiectasia
,
telangiectasis
,
cerebellar ataxia
,
hypoparathyroidism
,
pregnancy rate
,
defense mechanisms
,
proteinuria
,
ototoxicity
,
agammaglobulinemia
,
leukocyte-adhesion deficiency syndrome
,
hereditary congenital and neonatal diseases and abnormalities
,
radius fractures
,
fracture healing
,
wrist fractures
,
bariatric surgery
,
gastric bypass
,
gastrectomy
,
premenopause
,
osteoporotic fractures
,
hashimoto disease
,
giant cell arteritis
,
polymyalgia rheumatica
,
hypersensitivity
,
leukocytoclastic vasculitis cutaneous
,
chronic disease
,
cerebrovascular disorders
,
pituitary neoplasms
,
sex cord-gonadal stromal tumors
,
sertoli-leydig cell tumor
,
nodular goiter
,
hyperplasia
,
pituitary diseases
,
leydig cell tumor
,
focal nodular hyperplasia
,
hamartoma
,
body weight
,
gastroenteritis
,
autonomic nervous system diseases
,
primary dysautonomias
,
hypoventilation
,
lipodystrophy
,
hyponatremia
,
anorexia
,
anorexia nervosa
,
bone density
,
osteogenesis
,
nerve compression syndromes
,
tooth diseases
,
charcot-marie-tooth disease
,
hereditary sensory and motor neuropathy
,
primary graft dysfunction
,
renal colic
,
colic
,
cataract
,
anxiety disorders
,
anxiety
,
microbiota
,
rare diseases
,
neurodegenerative diseases
,
congenital bone marrow failure syndromes
,
undiagnosed diseases
,
cardiomyopathies
,
eye abnormalities
,
uveomeningoencephalitic syndrome
,
tumor microenvironment
,
wounds and injuries
,
spinal cord injuries
,
echocardiography
,
hyperspectral imaging
,
primary ovarian insufficiency
,
premature menopause
,
hip fractures
,
femoral fractures
,
femoral neck fractures
,
chronic pain
,
muscle neoplasms
,
cystic fibrosis
,
laparoscopic cholecystectomy
,
bites and stings
,
bite force
,
female infertility
,
dyslipidemias
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