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Spark Therapeutics
Spark Therapeutics
(ONCE)
Spark Therapeutics, Inc. is a developer of gene therapy treatments, which treat debilitating genetic diseases. It is a subsidiary of Hoffmann-La Roche.
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Financial
Marketed Drugs
Clinical Trials
Financial
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Company Revenue
Quarterly
Quarterly
Annual
Annual
Projections
*Quarterly sales USD (in millions)
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Revenue by Drug
Marketed Drugs
Therapeutic Areas:
All
Classification:
All
Include Generics:
Trade Name
Drug Name
Approved
Patent Expires
Indication
Luxturna
Voretigene neparvovec
2017-12-19
Retinitis pigmentosa
,
Leber congenital amaurosis
Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Drug Name
Phase 1
Phase 2
Phase 3
Phase 4
Indication
Voretigene neparvovec
retinal dystrophies
Bevifimod
sickle cell anemia
,
neoplasms
,
colonic neoplasms
,
adenocarcinoma
,
systemic lupus erythematosus
,
colorectal neoplasms
,
agammaglobulinemia
,
primary immunodeficiency diseases
,
von willebrand diseases
,
alzheimer disease
,
graft vs host disease
,
thrombocytopenic purpura idiopathic
,
protein c deficiency
,
leukemia
,
myeloid leukemia acute
,
non-hodgkin lymphoma
,
lymphoma
,
precursor cell lymphoblastic leukemia-lymphoma
,
b-cell chronic lymphocytic leukemia
,
hodgkin disease
,
b-cell lymphoma marginal zone
,
follicular lymphoma
,
mantle-cell lymphoma
,
myeloid leukemia chronic-phase
,
large b-cell lymphoma diffuse
,
myeloid leukemia accelerated phase
,
burkitt lymphoma
,
large-cell lymphoma immunoblastic
,
hemophilia b
,
thrombotic thrombocytopenic purpura
,
chronic obstructive pulmonary disease
,
dementia
,
mucocutaneous lymph node syndrome
,
immunologic deficiency syndromes
,
hemophilia a
,
alpha 1-antitrypsin deficiency
,
disease
,
healthy volunteers/patients
Globulin, immune
healthy volunteers/patients
,
neoplasms
,
colonic neoplasms
,
adenocarcinoma
,
systemic lupus erythematosus
,
colorectal neoplasms
,
kidney diseases
,
iga glomerulonephritis
,
ovarian neoplasms
,
ovarian epithelial carcinoma
,
ascites
,
agammaglobulinemia
,
alzheimer disease
,
chronic inflammatory demyelinating polyradiculoneuropathy
,
polyradiculoneuropathy
,
thrombocytopenic purpura idiopathic
,
dementia
,
mucocutaneous lymph node syndrome
,
primary immunodeficiency diseases
,
immunologic deficiency syndromes
Demand
chronic obstructive pulmonary disease
,
lung diseases
,
obstructive lung diseases
,
respiratory aspiration
,
erectile dysfunction
,
asthma
,
breast neoplasms
,
circulating neoplastic cells
,
neoplasm metastasis
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