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Orchard Therapeutics
Orchard Therapeutics
(ORTX)
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Revenue by Drug
Marketed Drugs
Therapeutic Areas:
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Classification:
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Include Generics:
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Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
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Status:
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Phases:
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Drug Name
Phase 1
Phase 2
Phase 3
Phase 4
Indication
Atidarsagene autotemcel
metachromatic leukodystrophy
,
lysosomal storage diseases
Simoladagene autotemcel
severe combined immunodeficiency
,
immunologic deficiency syndromes
Aspartame
leukemia
,
neoplasms
,
atopic dermatitis
,
myeloid leukemia acute
,
multiple myeloma
,
lymphoma
,
plasma cell neoplasms
,
large b-cell lymphoma diffuse
,
type 2 diabetes mellitus
,
diabetes mellitus
,
recurrence
,
opioid-related disorders
,
alzheimer disease
,
huntington disease
,
eczema
,
dermatitis
,
b-cell chronic lymphocytic leukemia
,
lymphoid leukemia
,
covid-19
,
meningioma
,
inflammation
,
triple negative breast neoplasms
,
serogroup b neisseria meningitidis
,
crush injuries
,
urologic neoplasms
,
urinary bladder neoplasms
,
urologic diseases
,
urinary bladder diseases
,
down syndrome
,
syndrome
,
cognitive dysfunction
,
central nervous system neoplasms
,
solitary fibrous tumors
,
neurofibromatosis 1
,
neurofibromatoses
,
hemangioblastoma
,
hemangiopericytoma
,
neurofibroma
,
streptococcal infections
,
thyroid neoplasms
,
thyroid diseases
,
pain
,
breast neoplasms
,
sickle cell anemia
,
pneumonia
,
renal insufficiency
,
headache
,
meningitis
,
rheumatoid arthritis
,
arthritis
,
bacterial pneumonia
,
juvenile arthritis
,
psoriatic arthritis
,
ankylosing spondylitis
,
carotid artery diseases
,
atherosclerosis
,
ulcerative colitis
,
fever
,
meningococcal meningitis
,
stroke
,
thromboembolism
,
hiv infections
,
tuberculosis
,
acquired immunodeficiency syndrome
,
immune reconstitution inflammatory syndrome
,
seizures
,
alopecia areata
,
alopecia
,
hair diseases
,
healthy volunteers/patients
,
infections
,
communicable diseases
,
intraabdominal infections
,
smoking cessation
,
neuroendocrine tumors
,
islet cell adenoma
,
psychomotor agitation
,
schizophrenia
,
renal cell carcinoma
,
carcinoma
,
gaucher disease
,
tobacco use disorder
,
acromegaly
,
fatigue
Histone-arginine methyltransferase carm1
cholestasis
,
pruritus
,
pregnancy complications
,
intrahepatic cholestasis
,
sclerosing cholangitis
,
biliary liver cirrhosis
,
digestive system diseases
,
cholangitis
,
fragile x syndrome
Surlorian
healthy volunteers/patients
,
coronary artery disease
,
esophageal neoplasms
,
obesity
,
overweight
,
squamous cell carcinoma of head and neck
,
squamous cell carcinoma
,
chronic urticaria
,
urticaria
,
type 1 diabetes mellitus
,
triple negative breast neoplasms
,
ovarian epithelial carcinoma
,
gastrointestinal endoscopy
,
lung neoplasms
,
renal cell carcinoma
,
cholangiocarcinoma
,
neoplasms
,
endometrial neoplasms
,
carcinosarcoma
,
hypertension
,
sepsis
,
acute kidney injury
,
non-small-cell lung carcinoma
,
breast neoplasms
,
covid-19
,
prostatic neoplasms
,
ovarian neoplasms
,
small cell lung carcinoma
,
carcinoma
,
neoplasm metastasis
,
stomach neoplasms
,
urinary bladder neoplasms
,
human influenza
,
asthma
,
esophageal squamous cell carcinoma
,
hepatocellular carcinoma
,
liver neoplasms
,
hypertriglyceridemia
,
gastroesophageal reflux
,
esophagitis
,
respiratory distress syndrome
,
respiratory tract infections
,
infections
,
coronavirus infections
,
respiratory insufficiency
,
severe acute respiratory syndrome
,
virus diseases
,
exercise-induced asthma
,
bronchial spasm
,
exercise-induced allergies
,
disease progression
,
type 2 diabetes mellitus
,
diabetes mellitus
,
lung diseases
,
chronic obstructive pulmonary disease
,
obstructive lung diseases
,
renal insufficiency
,
kidney function tests
,
thrombosis
,
thromboembolism
,
atherosclerosis
,
systemic lupus erythematosus
,
post-traumatic stress disorders
,
combat disorders
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