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Mirum Pharmaceuticals
Mirum Pharmaceuticals
(MIRM)
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Clinical Trials
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Revenue by Drug
Marketed Drugs
Therapeutic Areas:
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Classification:
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Include Generics:
Trade Name
Drug Name
Approved
Patent Expires
Indication
Livmarli
Maralixibat
2021-09-29
2031-2040
Pruritus
,
Alagille syndrome
Cholbam
Cholic acid
2015-03-17
Zellweger syndrome
,
Inborn errors metabolism
Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Drug Name
Phase 1
Phase 2
Phase 3
Phase 4
Indication
Cholic acid
inborn errors steroid metabolism
,
cholestasis
,
peroxisomal disorders
,
zellweger syndrome
,
infantile refsum disease
,
adrenoleukodystrophy
,
refsum disease
Maralixibat
overweight
,
healthy volunteers/patients
,
substance withdrawal syndrome
,
biliary atresia
,
cholestasis
,
syndrome
,
alagille syndrome
,
liver diseases
,
intrahepatic cholestasis
,
pruritus
,
fibrosis
,
cystic fibrosis
,
constipation
Maralixibat chloride
overweight
,
healthy volunteers/patients
,
liver cirrhosis
,
biliary liver cirrhosis
,
substance withdrawal syndrome
,
biliary atresia
,
sclerosing cholangitis
,
cholangitis
,
syndrome
,
alagille syndrome
,
liver diseases
,
cholestasis
,
intrahepatic cholestasis
,
fibrosis
,
pruritus
,
cystic fibrosis
,
constipation
Benzocaine
amyotrophic lateral sclerosis
,
motor neuron disease
,
malaria
,
falciparum malaria
,
multiple sclerosis
,
relapsing-remitting multiple sclerosis
,
sclerosis
,
leukemia
,
myelodysplastic syndromes
,
hematologic neoplasms
,
neoplasms
,
lymphoma
,
preleukemia
,
cough
,
anemia
,
aplastic anemia
,
venous thromboembolism
,
thromboembolism
,
healthy volunteers/patients
,
hip fractures
,
myocardial infarction
,
st elevation myocardial infarction
,
infarction
,
pharyngitis
,
dengue
,
severe dengue
,
viral hemorrhagic fevers
,
hygiene
,
autonomic nervous system diseases
,
immune system diseases
,
skin diseases
,
eczematous skin diseases
,
hypersensitivity
,
immediate hypersensitivity
,
type 2 diabetes mellitus
,
diabetes mellitus
,
atopic dermatitis
,
eczema
,
dermatitis
,
acute coronary syndrome
,
kidney diseases
,
chronic kidney failure
VOLIXIBAT
overweight
,
healthy volunteers/patients
,
non-alcoholic fatty liver disease
,
fatty liver
,
alcoholic fatty liver
,
cholangitis
,
pregnancy complications
,
cholestasis
,
intrahepatic cholestasis
,
sclerosing cholangitis
,
biliary liver cirrhosis
Sodium chloride
healthy volunteers/patients
,
contraception
,
pregnancy
,
allergic rhinitis
,
rhinitis
,
allergic rhinitis seasonal
,
asthma
,
bronchitis
,
pulmonary eosinophilia
,
prostatic neoplasms
,
castration-resistant prostatic neoplasms
,
migraine disorders
,
sleep wake disorders
Aspartame
hiv
,
bronchiectasis
,
escherichia coli infections
,
gastroenteritis
,
pharmacokinetics
,
dental plaque
,
hydrogen-ion concentration
,
salivation
,
healthy volunteers/patients
,
xerostomia
,
sjogren's syndrome
,
ototoxicity
,
mucositis
,
glioblastoma
,
covid-19
,
pyruvate dehydrogenase complex deficiency disease
,
sepsis
,
malnutrition
,
child nutrition disorders
,
colonoscopy
,
obesity
,
type 2 diabetes mellitus
,
overweight
,
diabetes mellitus
,
glucose intolerance
,
body weight
,
insulin resistance
,
metabolic syndrome
,
weight loss
,
feeding behavior
,
glucose metabolism disorders
,
metabolic diseases
,
abdominal obesity
,
adiposity
,
dyslipidemias
,
prediabetic state
,
glucose tolerance test
,
cognition
,
fasting
,
type 1 diabetes mellitus
,
placebos
,
hypoglycemia
,
gastric bypass
,
congenital hyperinsulinism
,
nesidioblastosis
,
driving under the influence
,
glycogen storage disease type iii
,
glycogen storage disease
,
kidney transplantation
,
hyperglycemia
,
sleep deprivation
,
cardiovascular diseases
,
mortality
,
hypersensitivity
,
gastrointestinal microbiome
,
chronic disease
,
neoplasms
,
diet
,
adolescent development
,
acromegaly
,
appetitive behavior
,
microbiota
,
chronic periodontitis
,
periodontitis
,
thirst
,
pregnancy rate
,
atherosclerosis
,
appetite
,
intestinal absorption
,
taste
,
hypoxia
,
blood glucose self-monitoring
,
deglutition disorders
,
syndrome
,
thrombosis
,
inflammation
,
platelet aggregation
,
wounds and injuries
,
spinal cord injuries
,
cold temperature
,
sleep
,
blood pressure
,
vascular stiffness
,
aging
,
exercise tolerance
,
alcohol drinking
SHP626
overweight
,
healthy volunteers/patients
,
non-alcoholic fatty liver disease
,
fatty liver
,
alcoholic fatty liver
,
cholangitis
,
pregnancy complications
,
cholestasis
,
intrahepatic cholestasis
,
sclerosing cholangitis
,
biliary liver cirrhosis
Arm1
pharmacokinetics
,
chronic obstructive pulmonary disease
,
obstructive lung diseases
,
positron-emission tomography
,
anemia
,
alzheimer disease
,
diagnostic imaging
,
medical sociology
,
malnutrition
,
disease
,
drug interactions
,
electrocardiography
,
therapeutic equivalency
,
pharmacological phenomena
,
dietary fats
,
liver diseases
,
stomach neoplasms
,
hypophosphatemia
,
hematologic neoplasms
,
respiratory aspiration
,
cystic fibrosis
,
pseudomonas infections
,
biological availability
,
castration-resistant prostatic neoplasms
,
heart failure
,
non-small-cell lung carcinoma
,
lung neoplasms
,
breast neoplasms
,
postcoital contraception
,
ovulation inhibition
,
atrial fibrillation
,
eczema
,
parkinson disease
,
small cell lung carcinoma
,
ovarian neoplasms
,
multiple myeloma
,
plasma cell neoplasms
,
tinnitus
,
leukemia
,
bcr-abl positive chronic myelogenous leukemia
,
myeloid leukemia
,
heart diseases
,
cardiomyopathies
,
libido
,
leiomyoma
,
myofibroma
,
overactive urinary bladder
,
hormonal contraception
,
unplanned pregnancy
,
b-cell lymphoma
,
erythema
,
skin abnormalities
,
myocardial infarction
,
infarction
,
hiv infections
,
acquired immunodeficiency syndrome
,
magnetic resonance angiography
,
tinea pedis
,
left ventricular dysfunction
,
ventricular dysfunction
,
interstitial lung diseases
,
ovarian epithelial carcinoma
,
thyroid neoplasms
,
thyroid diseases
,
pancreatic neoplasms
,
varicose ulcer
,
ulcer
,
leg ulcer
,
dialysis
,
prostatic hyperplasia
,
hyperplasia
,
angina pectoris
,
stable angina
,
ischemic stroke
,
stroke
,
cerebral infarction
,
urologic neoplasms
,
head and neck neoplasms
,
thromboembolism
,
venous thromboembolism
,
pulmonary hypertension
,
thrombosis
,
hyperphosphatemia
,
lung diseases
,
prostatic neoplasms
,
hemorrhage
,
venous thrombosis
,
non-hodgkin lymphoma
,
lymphoma
,
chronic renal insufficiency
,
kidney diseases
,
surgical blood loss
,
acne vulgaris
,
endometriosis
,
vascular diseases
,
peripheral arterial disease
,
peripheral vascular diseases
,
postoperative hemorrhage
,
pulmonary embolism
,
embolism
,
cardiovascular diseases
,
hemophilia b
,
abscess
,
spinal cord injuries
,
pathologic constriction
,
renal artery obstruction
,
pain
,
bacterial infections
,
esophageal neoplasms
,
low back pain
,
back pain
,
intraabdominal infections
,
chagas disease
,
chronic progressive multiple sclerosis
,
blood coagulation disorders
,
hemostatic disorders
,
hormone replacement therapy
,
hyperlipidemias
,
hyperlipoproteinemias
,
choroidal neovascularization
,
myopia
,
degenerative myopia
,
pathologic neovascularization
,
metrorrhagia
,
aspiration pneumonia
,
lung abscess
,
pelvic pain
,
pelvic infection
,
pelvic inflammatory disease
,
dysmenorrhea
,
metabolic bone diseases
,
osteoporosis
,
premenstrual dysphoric disorder
,
diabetic nephropathies
,
proteinuria
,
follicular lymphoma
,
wounds and injuries
,
brain neoplasms
,
congenital abnormalities
,
cardiovascular abnormalities
,
onychomycosis
,
memory disorders
,
carotid stenosis
,
pulmonary arterial hypertension
,
burns
,
depression
,
depressive disorder
,
hypersensitivity
,
aortic valve stenosis
,
heart valve diseases
,
ventricular outflow obstruction
,
abdominal abscess
,
erectile dysfunction
,
contraception
,
neoplasms
,
hypertension
,
carcinoma
,
hemophilia a
,
infections
,
healthy volunteers/patients
,
renal cell carcinoma
,
communicable diseases
,
multiple sclerosis
,
pneumonia
,
common cold
,
sclerosis
,
essential hypertension
,
atopic dermatitis
,
dermatitis
,
liver neoplasms
,
pharyngitis
,
relapsing-remitting multiple sclerosis
,
hot flashes
,
hepatocellular carcinoma
,
urinary tract infections
,
diabetes mellitus
,
coronary artery disease
,
headache
,
type 2 diabetes mellitus
,
colorectal neoplasms
,
menorrhagia
,
postmenopause
,
hypogonadism
,
physiological sexual dysfunction
,
magnetic resonance imaging
,
neoplasm metastasis
,
coronary disease
,
acute coronary syndrome
,
myocardial ischemia
,
syndrome
,
tension-type headache
,
tonsillitis
,
ischemia
,
renal insufficiency
,
chronic bronchitis
,
bronchitis
,
acute disease
,
fibrosis
,
obesity
,
respiratory tract infections
,
fever
,
peripheral nervous system diseases
,
ischemic optic neuropathy
,
optic nerve diseases
,
macular edema
,
edema
,
macular degeneration
,
energy metabolism
,
sinusitis
,
maxillary sinusitis
,
allergic rhinitis
,
rhinitis
,
allergic rhinitis seasonal
,
medicated intrauterine devices
,
wound healing
,
gene expression
,
cell proliferation
,
constipation
,
central nervous system neoplasms
,
photoallergic dermatitis
,
phototoxic dermatitis
,
four-dimensional computed tomography
Arm2
neoplasms
,
cancer pain
,
melanoma
,
oncogenes
,
thrombocytopenic purpura idiopathic
,
thrombocytopenic purpura
,
purpura
,
leukemia
,
lymphoma
,
precursor cell lymphoblastic leukemia-lymphoma
,
multiple myeloma
,
plasma cell neoplasms
,
rheumatoid arthritis
,
arthritis
,
inflammation
,
cachexia
,
hepatitis c
,
chronic hepatitis c
,
chronic hepatitis b
,
hepatitis
,
chronic hepatitis
,
hepatitis a
,
overweight
,
anxiety disorders
,
social phobia
,
pruritus
,
covid-19
,
hiv infections
,
infections
,
acquired immunodeficiency syndrome
,
communicable diseases
,
rhinitis
,
immunologic deficiency syndromes
,
atrial fibrillation
,
macular degeneration
,
malaria
,
vivax malaria
,
thrombocytopenia
,
inflammatory breast neoplasms
,
non-small-cell lung carcinoma
,
lung neoplasms
,
systemic lupus erythematosus
,
cough
,
common cold
,
dyslipidemias
,
multiple sclerosis
,
relapsing-remitting multiple sclerosis
,
sclerosis
,
coronary disease
,
coronary artery disease
,
myocardial ischemia
,
heart diseases
,
atherosclerosis
,
recurrence
,
carcinoma
,
ovarian neoplasms
,
endometrial neoplasms
,
ovarian epithelial carcinoma
,
breast neoplasms
,
hypertension
,
osteoporosis
,
postmenopausal osteoporosis
,
alzheimer disease
,
hypersensitivity
,
dentin sensitivity
,
headache
,
tension-type headache
,
prostatic hyperplasia
,
hyperplasia
,
dysmenorrhea
,
mumps
,
measles
,
chickenpox
,
rubella
,
spinal cord injuries
,
erectile dysfunction
,
asthma
,
chronic obstructive pulmonary disease
,
lung diseases
,
migraine disorders
,
type 2 diabetes mellitus
,
acne vulgaris
,
diabetes mellitus
,
prostatic neoplasms
,
back pain
,
hemorrhage
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