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Mirum Pharmaceuticals
Mirum Pharmaceuticals
(MIRM)
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Clinical Trials
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Revenue by Drug
Marketed Drugs
Therapeutic Areas:
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Classification:
All
Include Generics:
Trade Name
Drug Name
Approved
Patent Expires
Indication
Livmarli
Maralixibat
2021-09-29
2031-2040
Pruritus
,
Alagille syndrome
Cholbam
Cholic acid
2015-03-17
Zellweger syndrome
,
Inborn errors metabolism
Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Drug Name
Phase 1
Phase 2
Phase 3
Phase 4
Indication
Cholic acid
neurofibromatosis 1
,
neurofibromatoses
,
neurofibroma
,
hyperlipidemias
,
central nervous system neoplasms
,
aging
,
clostridium infections
,
colonic neoplasms
,
rectal neoplasms
,
echolocation
,
hyperlipoproteinemia type iv
,
metabolic syndrome
,
hypertriglyceridemia
,
familial combined hyperlipidemia
,
liver function tests
,
gastric bypass
,
alcoholic hepatitis
,
parkinson disease
,
huntington disease
,
cardiovascular diseases
,
heart diseases
,
recurrence
,
alcoholic fatty liver
,
gastrointestinal diseases
,
digestive system diseases
,
liver neoplasms
,
lipodystrophy
,
lipoma
,
rheumatoid arthritis
,
arthritis
,
biliary tract diseases
,
barrett esophagus
,
heart failure
,
cystic fibrosis
,
covid-19
,
muscle spasticity
,
hereditary spastic paraplegia
,
paraplegia
,
irritable bowel syndrome
,
constipation
,
cardiomyopathies
,
disease progression
,
amyloidosis
,
neoplasm metastasis
,
radiation injuries
,
body weight
,
insulin resistance
,
amyotrophic lateral sclerosis
,
motor neuron disease
,
sclerosis
,
cleft palate
,
hypospadias
,
x-linked genetic diseases
,
smith-lemli-opitz syndrome
,
hypertelorism
,
hiv
,
pruritus
,
bile duct diseases
,
adolescent development
,
sarcoidosis
,
polycystic kidney diseases
,
autosomal dominant polycystic kidney
,
cysts
,
obstructive jaundice
,
jaundice
,
esophageal neoplasms
,
head and neck neoplasms
,
end stage liver disease
,
hepatitis d
,
coinfection
,
breast neoplasms
,
cholestasis
,
healthy volunteers/patients
,
intrahepatic cholestasis
,
colorectal neoplasms
,
cerebrotendinous xanthomatosis
,
xanthomatosis
,
hepatitis a
,
malnutrition
,
pregnancy complications
,
glucose intolerance
,
sclerosing cholangitis
,
peroxisomal disorders
,
zellweger syndrome
,
infantile refsum disease
,
adrenoleukodystrophy
,
refsum disease
,
neoplasms
,
adenomatous polyposis coli
,
nasopharyngeal neoplasms
,
adenoma
,
colitis
,
retinal detachment
,
dissociative disorders
,
chronic hepatitis c
,
duodenal neoplasms
,
inborn errors metabolism
,
inborn errors lipid metabolism
,
inborn errors steroid metabolism
,
pregnancy
,
inborn genetic diseases
,
sepsis
,
child nutrition disorders
,
ulcerative colitis
,
inflammation
,
pouchitis
,
thyroid diseases
,
hepatitis c
,
chronic hepatitis
,
acute cholecystitis
,
cholecystitis
,
acalculous cholecystitis
,
pancreatitis
,
psoriasis
,
biliary liver cirrhosis
,
liver diseases
,
cholangitis
,
fibrosis
,
liver cirrhosis
,
non-alcoholic fatty liver disease
,
fatty liver
,
type 2 diabetes mellitus
,
diabetes mellitus
,
gallstones
,
cholelithiasis
,
cholecystolithiasis
,
obesity
,
hepatitis
,
morbid obesity
,
syndrome
,
chemical and drug induced liver injury
,
dyspepsia
,
hyperbilirubinemia
,
gestational diabetes
,
overweight
,
autoimmune hepatitis
,
fatigue
,
adiposity
,
neonatal hyperbilirubinemia
,
malabsorption syndromes
,
lipid metabolism disorders
,
diarrhea
,
hemolysis
,
hemolytic anemia
,
chronic kidney failure
,
kidney diseases
,
short bowel syndrome
,
cardiac surgical procedures
,
metaplasia
,
precursor cell lymphoblastic leukemia-lymphoma
,
lymphoid leukemia
,
fontan procedure
,
infections
,
communicable diseases
,
dermatitis
,
brain neoplasms
,
sarcoma
,
germ cell and embryonal neoplasms
,
medulloblastoma
,
retinoblastoma
,
rhabdoid tumor
,
ewing sarcoma
,
rhabdomyosarcoma
,
primitive neuroectodermal tumors
,
hepatoblastoma
,
retinal neoplasms
,
neuroectodermal tumors
,
phenylketonurias
,
appetite regulation
,
ischemia
,
liver transplantation
,
reperfusion injury
,
gastroesophageal reflux
,
metabolism
,
biliary atresia
,
liver regeneration
,
polyps
,
hepatocellular carcinoma
,
cholangiocarcinoma
,
wounds and injuries
,
hepatomegaly
Chenodiol
cerebrotendinous xanthomatosis
,
xanthomatosis
Maralixibat
overweight
,
healthy volunteers/patients
,
alagille syndrome
,
syndrome
,
biliary liver cirrhosis
,
substance withdrawal syndrome
,
biliary atresia
,
sclerosing cholangitis
,
cholestasis
,
liver diseases
,
intrahepatic cholestasis
,
pruritus
Maralixibat chloride
overweight
,
healthy volunteers/patients
,
biliary liver cirrhosis
,
substance withdrawal syndrome
,
biliary atresia
,
sclerosing cholangitis
,
alagille syndrome
,
cholestasis
,
liver diseases
,
syndrome
,
intrahepatic cholestasis
,
pruritus
,
fibrosis
,
cystic fibrosis
,
constipation
Benzocaine
leukemia
,
hematologic neoplasms
,
cancer pain
,
non-hodgkin lymphoma
,
lymphoma
,
b-cell chronic lymphocytic leukemia
,
t-cell lymphoma
,
mantle-cell lymphoma
,
large b-cell lymphoma diffuse
,
lymphoid leukemia
,
oncogenes
,
neoplasms
,
colorectal neoplasms
,
colonic neoplasms
,
rectal neoplasms
,
non-small-cell lung carcinoma
,
lung neoplasms
,
sarcoma
,
atopic dermatitis
,
eczema
,
dermatitis
,
chronic renal insufficiency
,
kidney diseases
,
anemia
,
neoplasm metastasis
,
hyperparathyroidism
,
thrombocytopenic purpura idiopathic
,
thrombocytopenia
,
thrombocytopenic purpura
,
psoriasis
,
secondary hyperparathyroidism
,
primary hyperparathyroidism
,
hypercalcemia
,
chronic kidney failure
,
purpura
,
hematologic diseases
,
hemostatic disorders
,
psoriatic arthritis
,
arthritis
,
gout
Lornoxicam
neoplasms
,
precursor cell lymphoblastic leukemia-lymphoma
,
precursor t-cell lymphoblastic leukemia-lymphoma
,
multiple myeloma
,
plasma cell neoplasms
,
hodgkin disease
,
large b-cell lymphoma diffuse
,
mantle-cell lymphoma
,
renal cell carcinoma
,
t-cell leukemia
,
b-cell leukemia
,
lymphoma
,
breast neoplasms
,
non-hodgkin lymphoma
,
leukemia
,
lymphoid leukemia
,
b-cell lymphoma
,
sarcoma
,
non-small-cell lung carcinoma
,
neoplasm metastasis
,
osteosarcoma
,
b-cell chronic lymphocytic leukemia
,
osteoporosis
,
cerebrotendinous xanthomatosis
,
follicular lymphoma
,
kidney diseases
VOLIXIBAT
overweight
,
healthy volunteers/patients
,
non-alcoholic fatty liver disease
,
fatty liver
,
alcoholic fatty liver
,
cholestasis
,
pruritus
,
pregnancy complications
,
intrahepatic cholestasis
,
sclerosing cholangitis
,
biliary liver cirrhosis
,
digestive system diseases
,
cholangitis
Aspartame
cocaine-related disorders
,
muscular atrophy
,
spinal muscular atrophy
,
atrophy
,
syndrome
,
lambert-eaton myasthenic syndrome
,
myasthenia gravis
,
congenital myasthenic syndromes
,
muscle weakness
SHP626
overweight
,
healthy volunteers/patients
,
non-alcoholic fatty liver disease
,
fatty liver
,
alcoholic fatty liver
,
cholestasis
,
pruritus
,
pregnancy complications
,
intrahepatic cholestasis
,
sclerosing cholangitis
,
biliary liver cirrhosis
,
digestive system diseases
,
cholangitis
Histone-arginine methyltransferase carm1
neuroendocrine tumors
Surlorian
neuroendocrine tumors
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