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Mirum Pharmaceuticals
Mirum Pharmaceuticals
(MIRM)
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Clinical Trials
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Revenue by Drug
Marketed Drugs
Therapeutic Areas:
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Classification:
All
Include Generics:
Trade Name
Drug Name
Approved
Patent Expires
Indication
Livmarli
Maralixibat
2021-09-29
2031-2040
Pruritus
,
Alagille syndrome
Cholbam
Cholic acid
2015-03-17
Zellweger syndrome
,
Inborn errors metabolism
Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Drug Name
Phase 1
Phase 2
Phase 3
Phase 4
Indication
Cholic acid
biliary liver cirrhosis
,
inborn errors steroid metabolism
,
cholestasis
,
peroxisomal disorders
,
zellweger syndrome
,
infantile refsum disease
,
adrenoleukodystrophy
,
refsum disease
Chenodiol
healthy volunteers/patients
,
liver diseases
,
hepatic insufficiency
,
echolocation
,
hyperlipidemias
,
hyperlipoproteinemia type iv
,
metabolic syndrome
,
hypertriglyceridemia
,
familial combined hyperlipidemia
,
syndrome
,
muscle spasticity
,
hereditary spastic paraplegia
,
paraplegia
,
liver cirrhosis
,
irritable bowel syndrome
,
constipation
,
covid-19
,
inborn genetic diseases
,
duchenne muscular dystrophy
,
muscular diseases
,
nervous system diseases
,
x-linked genetic diseases
,
muscular dystrophies
,
neuromuscular diseases
,
atrophic muscular disorders
,
cerebrotendinous xanthomatosis
,
xanthomatosis
,
biliary liver cirrhosis
,
fibrosis
,
obesity
,
malabsorption syndromes
,
morbid obesity
,
gallstones
,
cholelithiasis
,
cholecystolithiasis
,
diarrhea
,
dermatitis
,
type 2 diabetes mellitus
,
peroxisomal disorders
,
zellweger syndrome
,
infantile refsum disease
,
adrenoleukodystrophy
,
refsum disease
Maralixibat
overweight
,
healthy volunteers/patients
,
liver diseases
,
biliary liver cirrhosis
,
substance withdrawal syndrome
,
alagille syndrome
,
cholestasis
,
intrahepatic cholestasis
,
syndrome
,
pruritus
,
biliary atresia
,
sclerosing cholangitis
,
fibrosis
,
cystic fibrosis
,
constipation
Maralixibat chloride
overweight
,
healthy volunteers/patients
,
alagille syndrome
,
liver diseases
,
syndrome
,
biliary liver cirrhosis
,
substance withdrawal syndrome
,
cholestasis
,
intrahepatic cholestasis
,
biliary atresia
,
sclerosing cholangitis
,
pruritus
Benzocaine
anxiety disorders
,
healthy volunteers/patients
,
huntington disease
,
non-alcoholic fatty liver disease
,
overweight
,
fatty liver
,
hepatitis b
,
syndrome
,
breast neoplasms
,
neoplasms
,
chronic hepatitis b
,
chronic hepatitis
,
parkinson disease
,
eosinophilic esophagitis
,
pruritus
,
biliary liver cirrhosis
,
cholestasis
,
asthma
,
pulmonary hypertension
,
pulmonary arterial hypertension
,
diffuse scleroderma
,
sclerosis
,
myalgia
,
liver diseases
,
short bowel syndrome
,
myocardial infarction
,
drug resistance
,
heat stress disorders
,
mood disorders
,
combat disorders
,
traumatic stress disorders
,
gastrointestinal diseases
,
constipation
,
intestinal diseases
,
knee osteoarthritis
,
pain
,
osteoarthritis
,
musculoskeletal diseases
,
urinary bladder neoplasms
,
transitional cell carcinoma
,
depressive disorder
,
hepatitis
,
depression
,
major depressive disorder
,
hepatitis a
,
arthritis
,
anemia
,
kidney diseases
,
hepatitis c
,
cardiovascular diseases
,
chronic renal insufficiency
,
chronic hepatitis c
,
papillomavirus infections
,
hypertension
,
inflammation
,
pulmonary embolism
,
embolism
,
thromboembolism
,
thrombosis
,
venous thrombosis
,
infections
,
papillomavirus vaccines
,
meningitis
,
meningococcal infections
,
heart failure
,
glucose metabolism disorders
,
metabolic diseases
,
vascular diseases
,
heart diseases
,
metabolic syndrome
,
endocrine system diseases
,
hypertriglyceridemia
,
rheumatoid arthritis
,
atrial fibrillation
,
type 2 diabetes mellitus
,
diabetes mellitus
,
myositis
,
systemic scleroderma
,
juvenile arthritis
,
behcet syndrome
,
dermatomyositis
,
ankylosing spondylitis
,
sjogren's syndrome
,
systemic lupus erythematosus
,
herpes zoster
,
spondylarthritis
,
systemic vasculitis
,
diabetic neuropathies
,
hypercholesterolemia
,
facial pain
,
facial nerve diseases
,
facies
,
wasting syndrome
,
cachexia
,
keratoconjunctivitis sicca
,
dry eye syndromes
Lornoxicam
leukemia
,
myelodysplastic syndromes
,
hematologic neoplasms
,
graft vs host disease
,
preleukemia
,
syndrome
VOLIXIBAT
overweight
,
healthy volunteers/patients
,
non-alcoholic fatty liver disease
,
fatty liver
,
alcoholic fatty liver
,
cholestasis
,
pruritus
,
pregnancy complications
,
intrahepatic cholestasis
,
sclerosing cholangitis
,
biliary liver cirrhosis
,
digestive system diseases
,
cholangitis
Aspartame
medical sociology
,
infections
,
renal insufficiency
,
venous thrombosis
,
salivary gland neoplasms
,
breast neoplasms
,
neoplasms
,
colorectal neoplasms
,
non-small-cell lung carcinoma
,
thyroid neoplasms
,
sarcoma
,
melanoma
,
biliary tract neoplasms
,
obstructive sleep apnea
,
sleep apnea syndromes
,
apnea
,
chronic renal insufficiency
,
kidney diseases
,
x-linked bulbo-spinal atrophy
,
heart failure
,
thromboembolism
,
non-hodgkin lymphoma
,
human experimentation
,
venous thromboembolism
,
lymphoma
,
contraception
,
pulmonary hypertension
,
pulmonary arterial hypertension
,
stroke
,
respiratory insufficiency
,
communicable diseases
,
rheumatic diseases
,
prostatic neoplasms
,
castration-resistant prostatic neoplasms
,
macular edema
,
retinal vein occlusion
,
wounds and injuries
,
wound healing
,
postmenopause
,
endometriosis
,
chronic pain
,
interstitial cystitis
,
pelvic pain
,
syndrome
SHP626
overweight
,
healthy volunteers/patients
,
non-alcoholic fatty liver disease
,
fatty liver
,
alcoholic fatty liver
,
cholestasis
,
pruritus
,
pregnancy complications
,
intrahepatic cholestasis
,
sclerosing cholangitis
,
biliary liver cirrhosis
,
digestive system diseases
,
cholangitis
Histone-arginine methyltransferase carm1
neoplasms
,
respiratory aspiration
,
thrombocytopenic purpura idiopathic
,
purpura
,
photosensitivity disorders
,
renal cell carcinoma
,
leukemia
,
precursor cell lymphoblastic leukemia-lymphoma
,
multiple myeloma
,
plasma cell neoplasms
,
healthy volunteers/patients
,
rheumatoid arthritis
,
fibrosis
,
idiopathic pulmonary fibrosis
,
pulmonary fibrosis
,
hyperplasia
,
cachexia
,
respiratory tract infections
,
overweight
,
tendon injuries
,
anxiety disorders
,
social phobia
,
pruritus
,
cancer pain
,
melanoma
,
oncogenes
,
covid-19
,
hepatitis c
,
chronic hepatitis c
,
chronic hepatitis b
,
hepatitis
,
chronic hepatitis
,
hepatitis a
,
acquired immunodeficiency syndrome
,
hiv infections
,
inflammatory breast neoplasms
,
atrial fibrillation
,
lymphoma
,
macular degeneration
,
depressive disorder
,
ovarian neoplasms
,
endometrial neoplasms
,
ovarian epithelial carcinoma
,
immunologic deficiency syndromes
,
tuberculosis
,
pulmonary tuberculosis
,
vivax malaria
,
thrombocytopenia
,
non-small-cell lung carcinoma
,
lung neoplasms
,
non-hodgkin lymphoma
,
systemic lupus erythematosus
,
depression
,
major depressive disorder
,
cough
,
common cold
,
dyslipidemias
,
multiple sclerosis
,
relapsing-remitting multiple sclerosis
,
sclerosis
,
coronary disease
,
coronary artery disease
,
myocardial ischemia
,
heart diseases
,
atherosclerosis
,
leiomyosarcoma
,
respiratory syncytial viruses
,
rhinitis
,
allergic rhinitis
,
allergic rhinitis perennial
,
breast neoplasms
,
hypertension
,
diabetes mellitus
,
alzheimer disease
,
malaria
,
falciparum malaria
,
postmenopausal osteoporosis
,
headache
,
prostatic hyperplasia
,
personal satisfaction
,
hypersensitivity
,
dentin sensitivity
,
tension-type headache
,
diabetic neuropathies
,
mood disorders
,
postoperative nausea and vomiting
,
vomiting
,
nausea
,
dental caries
,
dysmenorrhea
,
respiratory sounds
,
allergic rhinitis seasonal
,
mumps
,
measles
,
chickenpox
,
rubella
,
spinal cord injuries
,
asthma
,
erectile dysfunction
,
chronic obstructive pulmonary disease
,
lung diseases
,
infections
,
type 2 diabetes mellitus
,
migraine disorders
,
obstructive lung diseases
,
communicable diseases
,
acne vulgaris
,
bipolar disorder
,
infectious skin diseases
,
insulin resistance
,
prostatic neoplasms
,
bacterial infections
,
bacterial skin diseases
,
cellulitis
,
skin diseases
,
soft tissue infections
,
back pain
,
hemorrhage
,
avitaminosis
,
aging
Surlorian
diabetes mellitus
,
type 1 diabetes mellitus
,
obesity
,
endometrial hyperplasia
,
hyperplasia
,
hemophilia a
,
hemophilia b
,
measles
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