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Mirum Pharmaceuticals
Mirum Pharmaceuticals
(MIRM)
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Clinical Trials
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Revenue by Drug
Marketed Drugs
Therapeutic Areas:
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Classification:
All
Include Generics:
Trade Name
Drug Name
Approved
Patent Expires
Indication
Livmarli
Maralixibat
2021-09-29
2031-2040
Pruritus
,
Alagille syndrome
Cholbam
Cholic acid
2015-03-17
Zellweger syndrome
,
Inborn errors metabolism
Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Drug Name
Phase 1
Phase 2
Phase 3
Phase 4
Indication
Cholic acid
healthy volunteers/patients
,
type 2 diabetes mellitus
,
lymphoma
,
central nervous system neoplasms
,
hepatic insufficiency
,
alcoholic hepatitis
,
cardiovascular diseases
,
heart diseases
,
syndrome
,
lipodystrophy
,
cleft palate
,
hypospadias
,
x-linked genetic diseases
,
smith-lemli-opitz syndrome
,
hypertelorism
,
hiv
,
metabolic syndrome
,
alcoholic fatty liver
,
head and neck neoplasms
,
end stage liver disease
,
liver diseases
,
fatty liver
,
non-alcoholic fatty liver disease
,
peroxisomal disorders
,
zellweger syndrome
,
infantile refsum disease
,
adrenoleukodystrophy
,
refsum disease
,
inborn errors metabolism
,
inborn errors lipid metabolism
,
inborn errors steroid metabolism
,
cholestasis
,
psoriasis
,
dermatitis
,
hepatitis c
,
chronic hepatitis c
,
hepatitis
,
appetite regulation
,
metabolism
,
aging
,
malnutrition
,
fontan procedure
,
liver cirrhosis
,
fibrosis
,
diabetes mellitus
,
hepatocellular carcinoma
,
liver neoplasms
,
cholangiocarcinoma
Chenodiol
healthy volunteers/patients
,
hepatic insufficiency
,
echolocation
,
hyperlipidemias
,
hyperlipoproteinemia type iv
,
metabolic syndrome
,
hypertriglyceridemia
,
familial combined hyperlipidemia
,
syndrome
,
liver diseases
,
cholangitis
,
lipodystrophy
,
familial partial lipodystrophy
,
muscle spasticity
,
hereditary spastic paraplegia
,
paraplegia
,
irritable bowel syndrome
,
constipation
,
biliary atresia
,
biliary liver cirrhosis
,
cerebrotendinous xanthomatosis
,
xanthomatosis
,
liver cirrhosis
,
fibrosis
,
non-alcoholic fatty liver disease
,
fatty liver
,
obesity
,
malabsorption syndromes
,
morbid obesity
,
gallstones
,
cholelithiasis
,
cholecystolithiasis
,
diarrhea
,
dermatitis
,
type 2 diabetes mellitus
,
peroxisomal disorders
,
zellweger syndrome
,
infantile refsum disease
,
adrenoleukodystrophy
,
refsum disease
Maralixibat
overweight
,
healthy volunteers/patients
,
syndrome
,
alagille syndrome
,
liver cirrhosis
,
fibrosis
,
biliary liver cirrhosis
,
substance withdrawal syndrome
,
biliary atresia
,
sclerosing cholangitis
,
cholangitis
,
liver diseases
,
cholestasis
,
intrahepatic cholestasis
,
pruritus
Maralixibat chloride
overweight
,
healthy volunteers/patients
,
syndrome
,
alagille syndrome
,
liver cirrhosis
,
fibrosis
,
biliary liver cirrhosis
,
substance withdrawal syndrome
,
biliary atresia
,
sclerosing cholangitis
,
cholangitis
,
liver diseases
,
cholestasis
,
intrahepatic cholestasis
,
pruritus
Benzocaine
pancreatic neoplasms
,
adenocarcinoma
Lornoxicam
sarcoma
,
hiv
,
acquired immunodeficiency syndrome
,
kaposi sarcoma
,
human herpesvirus 8
VOLIXIBAT
overweight
,
healthy volunteers/patients
,
non-alcoholic fatty liver disease
,
fatty liver
,
alcoholic fatty liver
,
cholangitis
,
pregnancy complications
,
cholestasis
,
intrahepatic cholestasis
,
sclerosing cholangitis
,
biliary liver cirrhosis
Sodium chloride
acute kidney injury
Aspartame
medical sociology
,
renal insufficiency
,
thrombosis
,
venous thrombosis
,
neoplasms
,
obstructive sleep apnea
,
sleep apnea syndromes
,
apnea
,
chronic renal insufficiency
,
kidney diseases
,
carcinoma
,
salivary gland neoplasms
,
heart failure
,
non-hodgkin lymphoma
,
lymphoma
,
infections
,
human experimentation
,
hypersensitivity
,
venous thromboembolism
,
thromboembolism
,
b-cell lymphoma
,
contraception
,
hypertension
,
pulmonary hypertension
,
pulmonary arterial hypertension
,
stroke
,
respiratory insufficiency
,
communicable diseases
,
rheumatic diseases
,
collagen diseases
,
prostatic neoplasms
,
castration-resistant prostatic neoplasms
,
macular edema
,
retinal vein occlusion
,
wounds and injuries
,
wound healing
,
edema
,
postmenopause
,
endometriosis
,
chronic pain
,
interstitial cystitis
,
pelvic pain
,
syndrome
SHP626
overweight
,
healthy volunteers/patients
,
non-alcoholic fatty liver disease
,
fatty liver
,
alcoholic fatty liver
,
cholangitis
,
pregnancy complications
,
cholestasis
,
intrahepatic cholestasis
,
sclerosing cholangitis
,
biliary liver cirrhosis
Arm1
breast neoplasms
,
neoplasm metastasis
Arm2
pharmacokinetics
,
chronic obstructive pulmonary disease
,
obstructive lung diseases
,
positron-emission tomography
,
anemia
,
alzheimer disease
,
diagnostic imaging
,
small cell lung carcinoma
,
medical sociology
,
renal insufficiency
,
drug interactions
,
electrocardiography
,
therapeutic equivalency
,
pharmacological phenomena
,
dietary fats
,
liver diseases
,
stomach neoplasms
,
hematologic neoplasms
,
respiratory aspiration
,
pain
,
biological availability
,
heart failure
,
non-small-cell lung carcinoma
,
lung neoplasms
,
postcoital contraception
,
ovulation inhibition
,
atrial fibrillation
,
breast neoplasms
,
multiple myeloma
,
plasma cell neoplasms
,
tinnitus
,
heart diseases
,
cardiomyopathies
,
cardiovascular diseases
,
parkinson disease
,
libido
,
leiomyoma
,
myofibroma
,
hormonal contraception
,
unplanned pregnancy
,
b-cell lymphoma
,
ovarian neoplasms
,
erythema
,
skin abnormalities
,
myocardial infarction
,
infarction
,
hiv infections
,
acquired immunodeficiency syndrome
,
magnetic resonance angiography
,
eczema
,
tinea pedis
,
pulmonary hypertension
,
left ventricular dysfunction
,
ventricular dysfunction
,
varicose ulcer
,
ulcer
,
leg ulcer
,
prostatic hyperplasia
,
hyperplasia
,
angina pectoris
,
stable angina
,
ischemic stroke
,
stroke
,
ischemia
,
cerebral infarction
,
urologic neoplasms
,
head and neck neoplasms
,
thromboembolism
,
venous thromboembolism
,
hemorrhage
,
lung diseases
,
surgical blood loss
,
thrombosis
,
venous thrombosis
,
non-hodgkin lymphoma
,
lymphoma
,
chronic renal insufficiency
,
acne vulgaris
,
prostatic neoplasms
,
hyperphosphatemia
,
kidney diseases
,
postoperative hemorrhage
,
pulmonary embolism
,
embolism
,
hemophilia b
,
abscess
,
endometriosis
,
vascular diseases
,
peripheral arterial disease
,
peripheral vascular diseases
,
bacterial infections
,
esophageal neoplasms
,
low back pain
,
back pain
,
intraabdominal infections
,
chagas disease
,
chronic progressive multiple sclerosis
,
blood coagulation disorders
,
hemostatic disorders
,
hormone replacement therapy
,
hyperlipidemias
,
hyperlipoproteinemias
,
choroidal neovascularization
,
myopia
,
degenerative myopia
,
pathologic neovascularization
,
metrorrhagia
,
aspiration pneumonia
,
lung abscess
,
pelvic pain
,
pelvic infection
,
pelvic inflammatory disease
,
dysmenorrhea
,
metabolic bone diseases
,
osteoporosis
,
premenstrual dysphoric disorder
,
diabetic nephropathies
,
proteinuria
,
follicular lymphoma
,
magnetic resonance imaging
,
brain neoplasms
,
onychomycosis
,
memory disorders
,
burns
,
depression
,
depressive disorder
,
spinal cord injuries
,
hypersensitivity
,
abdominal abscess
,
erectile dysfunction
,
contraception
,
hypertension
,
hemophilia a
,
neoplasms
,
infections
,
healthy volunteers/patients
,
pneumonia
,
common cold
,
communicable diseases
,
multiple sclerosis
,
pharyngitis
,
sclerosis
,
hot flashes
,
diabetes mellitus
,
headache
,
type 2 diabetes mellitus
,
relapsing-remitting multiple sclerosis
,
essential hypertension
,
menorrhagia
,
atopic dermatitis
,
dermatitis
,
renal cell carcinoma
,
carcinoma
,
acute coronary syndrome
,
coronary artery disease
,
syndrome
,
tension-type headache
,
tonsillitis
,
chronic bronchitis
,
bronchitis
,
acute disease
,
postmenopause
,
hypogonadism
,
physiological sexual dysfunction
,
colorectal neoplasms
,
urinary tract infections
,
obesity
,
coronary disease
,
myocardial ischemia
,
respiratory tract infections
,
fever
,
macular degeneration
,
energy metabolism
,
allergic rhinitis
,
rhinitis
,
allergic rhinitis seasonal
,
wound healing
,
gene expression
,
cell proliferation
,
constipation
,
neoplasm metastasis
,
central nervous system neoplasms
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