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Acer Therapeutics
Acer Therapeutics
(ACER)
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Trade Name
Drug Name
Approved
Patent Expires
Indication
Olpruva
Phenylbutyric acid
2022-12-22
Ornithine carbamoyltransferase deficiency disease
,
Carbamoyl-phosphate synthase i deficiency disease
,
Citrullinemia
,
Amyotrophic lateral sclerosis
Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Drug Name
Phase 1
Phase 2
Phase 3
Phase 4
Indication
Phenylbutyric acid
neoplasms
,
myeloproliferative disorders
,
myelodysplastic-myeloproliferative diseases
,
intestinal neoplasms
,
color vision defects
,
parkinson disease
,
drug-related side effects and adverse reactions
,
healthy volunteers/patients
,
congenital abnormalities
,
myelomonocytic leukemia chronic
,
leukemia myeloid chronic atypical bcr-abl negative
,
refractory anemia with excess of blasts
,
refractory anemia
,
myositis
,
inclusion body myositis
,
neuroblastoma
,
epilepsy
,
hyperammonemia
,
metabolic brain diseases inborn
,
leukemia
,
lymphoma
,
myelodysplastic syndromes
,
syndrome
,
myeloid leukemia acute
,
cystic fibrosis
,
muscular atrophy
,
spinal muscular atrophy
,
atrophy
,
preleukemia
,
myeloid leukemia
,
tuberculosis
,
pulmonary tuberculosis
,
fibrosis
,
brain diseases
,
hepatic encephalopathy
,
pyruvate dehydrogenase complex deficiency disease
,
spinal muscular atrophies of childhood
,
inborn errors amino acid metabolism
,
brain neoplasms
,
multiple acyl coenzyme a dehydrogenase deficiency
,
prostatic neoplasms
,
lung neoplasms
,
multiple myeloma
,
plasma cell neoplasms
,
plasmacytoma
,
beta-thalassemia
,
thalassemia
,
hiv infections
,
acquired immunodeficiency syndrome
,
liver cirrhosis
,
stomach neoplasms
,
head and neck neoplasms
,
lymphoproliferative disorders
,
epstein-barr virus infections
,
argininosuccinic aciduria
,
recurrence
,
mucinous adenocarcinoma
,
colonic neoplasms
,
adenocarcinoma
,
rectal neoplasms
,
cystadenocarcinoma
,
alzheimer disease
,
central nervous system diseases
,
nervous system diseases
,
spinal cord diseases
,
tdp-43 proteinopathies
,
neuromuscular diseases
,
ataxia
,
spinocerebellar degenerations
,
spinocerebellar ataxias
,
machado-joseph disease
,
cerebellar ataxia
,
huntington disease
,
inborn errors metabolism
,
corticobasal degeneration
,
wolfram syndrome
,
inborn errors lipid metabolism
,
deficiency diseases
,
amyotrophic lateral sclerosis
,
motor neuron disease
,
sclerosis
,
intrahepatic cholestasis
,
neurodegenerative diseases
,
inborn genetic diseases
,
cholestasis
,
proteinuria
,
maple syrup urine disease
,
hemophilia b
,
parkinsonian disorders
,
progressive supranuclear palsy
,
paralysis
,
inborn urea cycle disorders
,
diabetes mellitus
,
type 2 diabetes mellitus
,
insulin resistance
,
obesity
Celiprolol
ehlers-danlos syndrome
,
type iv ehlers-danlos syndrome
Bevifimod
small cell lung carcinoma
,
glioblastoma
,
merkel cell carcinoma
,
non-muscle invasive bladder neoplasms
,
thyroid neoplasms
,
burkitt lymphoma
,
pancreatic ductal carcinoma
,
neurofibromatosis 1
,
hereditary sensory and autonomic neuropathies
,
central nervous system neoplasms
,
brain diseases
,
neuroblastoma
,
ewing sarcoma
,
drug interactions
,
transitional cell carcinoma
,
uterine cervical neoplasms
,
urinary bladder neoplasms
,
brain concussion
,
post-concussion syndrome
,
astrocytoma
,
myeloproliferative disorders
,
b-cell chronic lymphocytic leukemia
,
t-cell lymphoma
,
t-cell lymphoma peripheral
,
t-cell lymphoma cutaneous
,
sarcoma
,
mycosis fungoides
,
squamous cell neoplasms
,
postoperative pain
,
precursor t-cell lymphoblastic leukemia-lymphoma
,
lyme neuroborreliosis
,
ocular hypertension
,
open-angle glaucoma
,
melanoma
,
multiple myeloma
,
brain neoplasms
,
recurrence
,
respiratory syncytial viruses
,
glioma
,
carcinoma
,
hepatocellular carcinoma
,
adenocarcinoma
,
plasma cell neoplasms
,
head and neck neoplasms
,
ovarian epithelial carcinoma
,
ovarian neoplasms
,
hodgkin disease
,
endometrial neoplasms
,
liver neoplasms
,
squamous cell carcinoma
,
atopic dermatitis
,
paraproteinemias
,
pancreatic neoplasms
,
osteoporosis
,
stomach neoplasms
,
esophageal neoplasms
,
hematopoietic stem cell transplantation
,
fallopian tube neoplasms
,
peritoneal neoplasms
,
human influenza
,
oligodendroglioma
,
myelodysplastic syndromes
,
inflammation
,
macular edema
,
diabetic retinopathy
,
eczema
,
skin diseases
,
plasmacytoma
,
plasma cell leukemia
,
disease progression
,
motor activity
,
overactive urinary bladder
,
keratoconjunctivitis sicca
,
dry eye syndromes
,
communicable diseases
,
interstitial cystitis
,
meningococcal infections
,
meningococcal meningitis
,
meningitis
,
serogroup b neisseria meningitidis
,
hematologic diseases
,
immune system diseases
,
blood protein disorders
,
lymphoproliferative disorders
,
vascular diseases
,
neoplasms by histologic type
,
immunoproliferative disorders
,
hemorrhagic disorders
,
asthma
,
waldenstrom macroglobulinemia
,
skin neoplasms
,
myeloid leukemia
,
malignant mesothelioma
,
mesothelioma
,
sickle cell anemia
,
hemolysis
,
monocytic leukemia acute
,
irritable bowel syndrome
,
facial pain
,
small fiber neuropathy
,
myelomonocytic leukemia chronic
,
discoid lupus erythematosus
,
cutaneous lupus erythematosus
,
meningeal neoplasms
,
breast neoplasms
,
colorectal neoplasms
,
non-small-cell lung carcinoma
,
lymphoma
,
myeloid leukemia acute
,
prostatic neoplasms
,
renal cell carcinoma
,
squamous cell carcinoma of head and neck
,
coronavirus infections
,
non-hodgkin lymphoma
,
colonic neoplasms
,
neoplasm metastasis
,
large b-cell lymphoma diffuse
,
b-cell lymphoma
,
rectal neoplasms
,
psoriatic arthritis
,
follicular lymphoma
,
infections
,
lyme disease
,
juvenile arthritis
,
lung neoplasms
,
borrelia infections
,
rectal diseases
,
crohn disease
,
neuralgia
,
partial epilepsies
,
kidney neoplasms
,
male breast neoplasms
,
respiratory tract infections
,
bacterial infections
,
infectious skin diseases
,
wound infection
,
soft tissue infections
,
cellulitis
,
gastrointestinal neoplasms
,
digestive system neoplasms
,
gastrointestinal diseases
,
intestinal neoplasms
,
digestive system diseases
,
colonic diseases
,
intestinal diseases
,
pruritus
,
chronic renal insufficiency
,
chronic kidney failure
,
obesity
,
endocrine system diseases
,
fetal growth retardation
,
growth disorders
,
hematologic neoplasms
,
invasive pulmonary aspergillosis
,
neuroaspergillosis
,
neutropenia
,
fever
,
febrile neutropenia
,
hyperthermia
,
amyloid plaque
,
bronchiolitis obliterans syndrome
,
lymphoid leukemia
,
restless legs syndrome
,
sleep deprivation
,
complex partial epilepsy
,
metabolic syndrome
,
abdominal obesity
,
pneumococcal infections
,
vector borne diseases
,
immunization
,
residual neoplasm
,
carpal tunnel syndrome
,
aplastic anemia
,
polyneuropathies
,
delirium
,
liver cirrhosis
,
muscle cramp
,
lung diseases
,
virus diseases
,
coronaviridae infections
,
neoplasms by site
,
rheumatoid arthritis
,
neoplasms
,
covid-19
,
healthy volunteers/patients
,
hemophilia a
,
leukemia
,
psoriasis
,
candidemia
,
precursor cell lymphoblastic leukemia-lymphoma
,
type 2 diabetes mellitus
,
hemophilia b
,
pain
,
ankylosing spondylitis
,
pituitary dwarfism
,
candidiasis
,
aspergillosis
,
invasive candidiasis
,
diabetes mellitus
,
arthritis
,
kidney transplantation
,
precursor b-cell lymphoblastic leukemia-lymphoma
,
schizophrenia
,
laron syndrome
,
respiratory tract diseases
,
mycoses
,
pharmacokinetics
,
pneumonia
,
postherpetic neuralgia
,
cardiovascular diseases
,
axial spondyloarthritis
,
brain injuries
,
type 1 diabetes mellitus
,
insulin resistance
,
hemostatic disorders
,
diabetic neuropathies
,
anxiety disorders
,
ventilator-associated pneumonia
,
relapsing-remitting multiple sclerosis
,
tremor
,
essential tremor
,
atherosclerosis
,
non-radiographic axial spondyloarthritis
,
electrocardiography
,
smoking cessation
,
traumatic brain injuries
,
dwarfism
,
self concept
,
pathologic constriction
,
spinal stenosis
,
abdominal pain
,
tissue adhesions
,
fibromyalgia
,
sepsis
,
obsessive-compulsive disorder
,
rheumatic fever
,
liver diseases
,
agnosia
,
anxiety
,
neisseria meningitidis
,
ulcerative colitis
,
inflammatory bowel diseases
,
fatty liver
,
metabolism
,
metabolic bone diseases
,
healthcare-associated pneumonia
,
drug-related side effects and adverse reactions
,
sars-cov-2
,
uremia
,
hypercholesterolemia
,
coronary disease
,
coronary artery disease
,
myocardial ischemia
,
heart failure
,
amyloidosis
,
vaccination
Zotiraciclib
multiple sclerosis
,
disease progression
,
neoplasm metastasis
,
autoimmune diseases
,
nervous system diseases
,
autoimmune diseases of the nervous system
,
chronic progressive multiple sclerosis
,
sclerosis
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